日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

A prime editing strategy to rewrite the γ-globin promoters and reactivate fetal hemoglobin for sickle cell disease

镰状细胞病的主要编辑策略是重写γ-珠蛋白启动子并重新激活胎儿血红蛋白。

Chalumeau, Anne; Bou Dames, Maria; Fontana, Letizia; Amistadi, Simone; Antoniou, Panagiotis; Loganathan, Priyanka; Mombled, Margaux; Corre, Guillaume; Peterka, Martin; Amendola, Mario; Giovannangeli, Carine; Maresca, Marcello; Miccio, Annarita; Brusson, Mégane

Dual inhibition of DNA-PK and PolÏ´ boosts precision of diverse prime editing systems.

DNA-PK 和 PolÏ´ 的双重抑制提高了各种主要编辑系统的精确度

Dacquay Louis C, Antoniou Panagiotis, Mentani Astrid, Selfjord Niklas, MÃ¥rtensson Hanna, Hsieh Pei-Pei, Mustfa Salman, Thom George, Wimberger Sandra, Firth Mike, Akrap Nina, Maresca Marcello, Peterka Martin

Harnessing DSB repair to promote efficient homology-dependent and -independent prime editing

利用DSB修复促进高效的同源依赖性和非同源性起始编辑

Peterka, Martin; Akrap, Nina; Li, Songyuan; Wimberger, Sandra; Hsieh, Pei-Pei; Degtev, Dmitrii; Bestas, Burcu; Barr, Jack; van de Plassche, Stijn; Mendoza-Garcia, Patricia; Šviković, Saša; Sienski, Grzegorz; Firth, Mike; Maresca, Marcello