ImmTOR nanoparticles enhance AAV transgene expression after initial and repeat dosing in a mouse model of methylmalonic acidemia
在甲基丙二酸血症小鼠模型中,ImmTOR纳米颗粒在首次和重复给药后可增强AAV转基因的表达。
期刊:Molecular Therapy-Methods & Clinical Development
影响因子:4.7
doi:10.1016/j.omtm.2021.06.015
Ilyinskii, Petr O; Michaud, Alicia M; Rizzo, Gina L; Roy, Christopher J; Leung, Sheldon S; Elkins, Stephanie L; Capela, Teresa; Chowdhury, Aparajita; Li, Lina; Chandler, Randy J; Manoli, Irini; Andres-Mateos, Eva; Johnston, Lloyd P M; Vandenberghe, Luk H; Venditti, Charles P; Kishimoto, Takashi Kei