Phase 1 Open-Label Study of Omigapil in Patients With LAMA2- or COL6-Related Dystrophy
奥米加匹治疗 LAMA2 或 COL6 相关肌营养不良症患者的 1 期开放标签研究
期刊:Neurology-Genetics
影响因子:3.7
doi:10.1212/NXG.0000000000200148
Foley, A Reghan; Yun, Pomi; Leach, Meganne E; Neuhaus, Sarah B; Averion, Gilberto V; Hu, Ying; Hayes, Leslie H; Donkervoort, Sandra; Jain, Minal S; Waite, Melissa; Parks, Rebecca; Bharucha-Goebel, Diana X; Mayer, Oscar H; Zou, Yaqun; Fink, Margaret; DeCoster, Jameice; Mendoza, Christopher; Arévalo, Cynthia; Hausmann, Rudolf; Petraki, Diana; Cheung, Ken; Bönnemann, Carsten G