日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Efficacy and safety of marstacimab prophylaxis in hemophilia A/B with inhibitors: results from the phase 3 BASIS trial

marstacimab预防治疗A/B型血友病伴抑制剂的疗效和安全性:来自3期BASIS试验的结果

Matino, Davide; Acharya, Suchitra S; Taylor, Carrie Turich; Sun, Pengling; Agathon, Delphine; Raje, Sangeeta; Gould, Travis; Palladino, Andrew; Mahlangu, Johnny; Lissitchkov, Toshko; Todorova, Mariya; Chan, Anthony; Carcao, Manuel; Sun, Jing; Yang, Renchi; Wu, Runhui; Jin, Chenghao; Zeng, Xiaojing; Boban, Ana; Bilic, Ernest; Frenzel, Laurent; Fung Chan, Godfrey Chi; Kong Li, Chi; Apte, Shashikant; Choraria, Nirmalkumar; Chistolini, Antonio; Marchesini, Emanuela; Peyvandi, Flora; Fujii, Teruhisa; Matsushita, Tadashi; Kaneda, Makoto; Lyu, Chuhl Joo; Park, Young Shil; Kim, SungEun; Martinez, Laura Villarreal; Adrian, Javier Morales; Wali, Yasser; Al Khabori, Murtadha; Kurtov, Igor; Alzahrani, Hazzaa; Zaher, Galila; Micic, Dragan; Miljic, Predrag; Kostic, Gordana; Vucic, Miodrag; Djurdjevic, Predrag; Hidalgo, Olga Benitez; Porras, Jose Gonzalez; Jiménez-Yuste, Víctor; Calvo Villas, Jose Manuel; Lopez Fernandez, Maria Fernanda; Albayrak, Canan; Okan, Vahap; Balkan, Can; Sahin, Fahri; Antmen, Ali; Unal, Ekrem; Visweshwar, Nathan; Sharathkumar, Anjali; Kruse-Jarres, Rebecca

Historical, current and future treatments for von Willebrand disease

血管性血友病的历史、现状和未来治疗方法

Casari, Caterina; Leebeek, Frank W G; Peyvandi, Flora

Genetic determinants of clinical variability in type 2 von Willebrand disease: bridging genotype and phenotype

2型血管性血友病临床变异的遗传决定因素:连接基因型和表型

Seidizadeh, Omid; Ciavarella, Alessandro; Baronciani, Luciano; Colpani, Paola; Cairo, Andrea; Siboni, Simona Maria; Peyvandi, Flora

Association of SARS-CoV-2 infection with long-lasting increase in circulating IL-32 levels

SARS-CoV-2感染与循环IL-32水平长期升高相关

Miano, Lorenzo; Sinopoli, Elena; Cherubini, Alessandro; Suffritti, Chiara; Pelusi, Serena; Rahmeh, Fatima; Lamorte, Giuseppe Enzo; Peyvandi, Flora; Blasi, Francesco; Grasselli, Giacomo; Bandera, Alessandra; Gualtierotti, Roberta; Prati, Daniele; Valenti, Luca Vittorio Carlo

IFNAR2 p.F8S Variant Associates with Severe COVID-19 and Adaptive Immune Cell Activation Modulation

IFNAR2 p.F8S 变异与重症 COVID-19 和适应性免疫细胞活化调节相关

Malvestiti, Francesco; Lombardi, Angela; Gentile, Francesco; Torcianti, Veronica; Trombetta, Elena; Cherubini, Alessandro; Lamorte, Giuseppe; Uceda Renteria, Sara Colonia; Marchelli, Daniele; Rosso, Lorenzo; Bandera, Alessandra; Peyvandi, Flora; Blasi, Francesco; Grasselli, Giacomo; Porretti, Laura; Alqahtani, Saleh; Prati, Daniele; Gualtierotti, Roberta; Soskic, Blagoje; Vaira, Valentina; Ronzoni, Luisa; Valenti, Luca

Single Cell Analysis Reveals the Presence of Novel Intermediate Cells in Both Mice and Patients With Severe MASLD

单细胞分析揭示了小鼠和重症MASLD患者体内均存在新型中间细胞。

Meroni, Marica; Pelucchi, Paride; Paolini, Erika; Longo, Miriam; Sula, Ada; Battistin, Michele; Chiodi, Alice; Mattinzoli, Deborah; Ikehata, Masami; Trombetta, Elena; Dondossola, Daniele; Mezzelani, Alessandra; Tartaglia, Gianluca Martino; Castellano, Giuseppe; Fracanzani, Anna Ludovica; Peyvandi, Flora; Gatti, Stefano; Mosca, Ettore; Dongiovanni, Paola

Updated global prevalence and ethnic diversity of von Willebrand disease based on population genetics analysis

基于群体遗传学分析的最新全球血管性血友病患病率和种族多样性

Seidizadeh, Omid; Cairo, Andrea; Oriani, Camilla; Peyvandi, Flora

Corrigendum to 'Deep molecular modeling and mechanistic insights into type 2A von Willebrand disease with von Willebrand factor A2 domain mutations': [Research and Practice in Thrombosis and Haemostasis 9(7) (2025) 103233]

对“具有血管性血友病因子 A2 结构域突变的 2A 型血管性血友病的深度分子建模和机制见解”的更正:[血栓与止血研究与实践 9(7) (2025) 103233]

Seidizadeh, Omid; Mollica, Luca; Giana, Davide; Baronciani, Luciano; Colpani, Paola; Sicuro, Lea; Cairo, Andrea; Peyvandi, Flora

Durability of efficacy, safety, and quality of life 5 years after valoctocogene roxaparvovec gene transfer for severe hemophilia A: final phase 3 GENEr8-1 trial results

接受valoctocogene roxaparvovec基因转移治疗重度A型血友病5年后,疗效、安全性和生活质量的持久性:GENEr8-1 III期临床试验的最终结果

Leavitt, Andrew D; Mahlangu, Johnny; Raheja, Priyanka; Symington, Emily; Quon, Doris V; Giermasz, Adam; Kenet, Gili; Lowe, Gillian; Key, Nigel S; Millar, Carolyn M; Pipe, Steven W; Chou, Sheng-Chieh; Klamroth, Robert; Mason, Jane; Chambost, Hervé; Peyvandi, Flora; Majerus, Elaine; Pepperell, Dominic; Tan, Chee Wee; Yu, Hua; Chavele, Konstantia-Maria; Ozelo, Margareth C

Beyond a century of discovery: the global and persistent burden of underdiagnosis in von Willebrand disease

一个世纪以来的发现:血管性血友病漏诊的全球性和持续性负担

Seidizadeh, Omid; Abdul-Kadir, Rezan; Mannucci, Pier Mannuccio; Peyvandi, Flora