A new dystrophin-deficient rat model mirroring exon skipping in patients with DMD exon 45 deletions
一种新的肌营养不良蛋白缺陷大鼠模型,模拟了DMD患者45号外显子缺失中的外显子跳跃现象
期刊:Disease Models & Mechanisms
影响因子:3.3
doi:10.1242/dmm.052578
Wang, Tao; Daoud, Cynthia; Dubois, Auriane; Corre, Guillaume; Bellec, Jessica; Bovolenta, Matteo; Philidet, Louise; Dorval, Alan; Bourg, Nathalie; Roudaut, Carinne; Albini, Sonia; Warthi, Ganesh; Jaber, Abbass; Richard, Isabelle