Effect of Poloxamer 188 vs Placebo on Painful Vaso-Occlusive Episodes in Children and Adults With Sickle Cell Disease: A Randomized Clinical Trial
泊洛沙姆188与安慰剂对镰状细胞病儿童和成人疼痛性血管阻塞发作的影响:一项随机临床试验
期刊:Journal of the American Medical Association
影响因子:55
doi:10.1001/jama.2021.3414
Casella, James F; Barton, Bruce A; Kanter, Julie; Black, L Vandy; Majumdar, Suvankar; Inati, Adlette; Wali, Yasser; Drachtman, Richard A; Abboud, Miguel R; Kilinc, Yurdanur; Fuh, Beng R; Al-Khabori, Murtadha K; Takemoto, Clifford M; Salman, Emad; Sarnaik, Sharada A; Shah, Nirmish; Morris, Claudia R; Keates-Baleeiro, Jennifer; Raj, Ashok; Alvarez, Ofelia A; Hsu, Lewis L; Thompson, Alexis A; Sisler, India Y; Pace, Betty S; Noronha, Suzie A; Lasky, Joseph L 3rd; de Julian, Elena Cela; Godder, Kamar; Thornburg, Courtney Dawn; Kamberos, Natalie L; Nuss, Rachelle; Marsh, Anne M; Owen, William C; Schaefer, Anne; Tebbi, Cameron K; Chantrain, Christophe F; Cohen, Debra E; Karakas, Zeynep; Piccone, Connie M; George, Alex; Fixler, Jason M; Singleton, Tammuella C; Moulton, Thomas; Quinn, Charles T; de Castro Lobo, Clarisse Lopes; Almomen, Abdulkareem M; Goyal-Khemka, Meenakshi; Maes, Philip; Emanuele, Marty; Gorney, Rebecca T; Padgett, Claire S; Parsley, Ed; Kronsberg, Shari S; Kato, Gregory J; Gladwin, Mark T