日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Adeno-Associated Virus Gene Transfer Ameliorates Progression of Skeletal Lesions in Mucopolysaccharidosis IVA Mice.

腺相关病毒基因转移可改善粘多糖贮积症IVA小鼠骨骼病变的进展

Herreño-Pachón Angélica María, Sawamoto Kazuki, Stapleton Molly, Khan Shaukat, Piechnik Matthew, Álvarez Jose Victor, Tomatsu Shunji

Evading the AAV Immune Response in Mucopolysaccharidoses

黏多糖贮积症中逃避AAV免疫反应

Piechnik, Matthew; Sawamoto, Kazuki; Ohnishi, Hidenori; Kawamoto, Norio; Ago, Yasuhiko; Tomatsu, Shunji