Repurposing drugs for treating the neurobehavioral manifestations of PTEN hamartoma tumor syndrome.
将药物重新用于治疗 PTEN 错构瘤肿瘤综合征的神经行为表现。
期刊:iScience
影响因子:4.1
doi:10.1016/j.isci.2026.115428
Fieblinger Tim, Rudolph Judith, Müller Kerstin, Friess Petra, Weigelt Nicole, Thiede Christina, Modolo Simone, Federico Denise, Majandinow Malik, Tinarelli Federico, Costantini Vivian J A, Marrese Pier P, Mercuri Annalisa, Carty Nikisha, Gomes Ana Christina, Whitehead Maria A, Gerrard Philip A, Papadopoulos Chrisovalantis, Elvin Paul