Mannose-coupled AAV2: A second-generation AAV vector for increased retinal gene therapy efficiency
甘露糖偶联 AAV2:可提高视网膜基因治疗效率的第二代 AAV 载体
期刊:Molecular Therapy-Methods & Clinical Development
影响因子:
doi:10.1016/j.omtm.2024.101187
Mathieu Mével, Virginie Pichard, Mohammed Bouzelha, Dimitri Alvarez-Dorta, Pierre-Alban Lalys, Nathalie Provost, Marine Allais, Alexandra Mendes, Elodie Landagaray, Jean-Baptiste Ducloyer, Estelle Toublanc, Anne Galy, Nicole Brument, Gaëlle M Lefevre, Sébastien G Gouin, Carolina Isiegas, Guylène Le