日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Advances in cystic fibrosis: CFTR modulator triple combinations

囊性纤维化治疗进展:CFTR调节剂三联疗法

Burgel, Pierre-Régis; Mall, Marcus A

Evaluating Long-Term Effectiveness of Cystic Fibrosis Modulator Therapies after Rapid Adoption: A Dual-Approach Study

快速推广应用后评估囊性纤维化调节剂疗法的长期疗效:一项双重方法研究

Miranda Afonso, Pedro; Zhou, Grace C; Su, Weiji; Burgel, Pierre-Régis; Cromwell, Elizabeth; Goss, Christopher H; Keogh, Ruth H; Liou, Theodore G; Marshall, Bruce C; Mayer-Hamblett, Nicole; Morgan, Wayne J; Ostrenga, Joshua S; Pasta, David J; Schechter, Michael S; Stanojevic, Sanja; Wainwright, Claire E; Szczesniak, Rhonda D; Andrinopoulou, Eleni-Rosalina

Benefit and risk associated with interleukin-6 receptor inhibitor administration during severe COVID-19: a retrospective multicentric study

重症 COVID-19 期间使用白细胞介素-6 受体抑制剂的获益和风险:一项回顾性多中心研究

Lefèvre, Charlène; Funck-Brentano, Théo; Cachanado, Marine; Plocque, Alexia; Youinou, Maëlle; Fels, Audrey; Pène, Frédéric; Savale, Laurent; Montani, David; Voisin, Olivier; Bintein, Flore; Wildenberg, Lucille; Philippe, Axel; Legriel, Stéphane; Roche, Nicolas; Burgel, Pierre-Régis; Tran, Marc; Noël, Nicolas; Baillard, Christophe; Duranteau, Jacques; Chatellier, Gilles; Philippart, Francois

Cystic Fibrosis Microbiome-directed Antibiotic Therapy Trial in Exacerbations Results Stratified (CFMATTERS): results of a multicentre randomised controlled trial

囊性纤维化急性加重期微生物组导向抗生素治疗试验结果分层分析(CFMATTERS):一项多中心随机对照试验的结果

Plant, Barry J; Einarsson, Gisli G; Deasy, Kevin F; Dahly, Darren; Singh, Pradeep K; Barry, Peter J; Goss, Christopher H; Fajac, Isabelle; Vagg, Tamara; Durieu, Isabelle; Flanagan, Evelyn; O'Callaghan, Grace; Martin, Clémence; Burgel, Pierre-Régis; Haworth, Charles S; Floto, R Andres; Downey, Damian G; Dupont, Lieven J; Jones, Andrew M; Elborn, J Stuart; Eustace, Joseph A; Mall, Marcus A; Tunney, Michael M

CFTR Modulators for the Treatment of Chronic Obstructive Pulmonary Disease: The Jury Is Still Out!

CFTR调节剂治疗慢性阻塞性肺病:疗效尚无定论!

Regard, Lucile; Burgel, Pierre-Régis

Elexacaftor-tezacaftor-ivacaftor in people with cystic fibrosis harbouring two CFTR Class I variants: real-world data from the French compassionate programme

在携带两个 CFTR I 类变异的囊性纤维化患者中使用 Elexacaftor-tezacaftor-ivacaftor:来自法国同情用药计划的真实世界数据

Burgel, Pierre-Régis; Girodon, Emmanuelle; Sharma, Neeraj; Raynal, Caroline; Da Silva, Jennifer; Sasorith, Souphatta; Martin, Clémence; Sermet-Gaudelus, Isabelle; Raraigh, Karen

Cystic fibrosis liver disease progression in the era of elexacaftor-tezacaftor-ivacaftor

囊性纤维化肝病在依来卡托-替扎卡托-伊伐卡托时代的进展

Mouliade, Charlotte; Parlati, Lucia; Tzedakis, Stylianos; Collier, Mathis; Bouam, Samir; Vallet-Pichard, Anais; D'Halluin-Venier, Valérie; Kanaan, Reem; Pol, Stanislas; Sogni, Philippe; Burgel, Pierre-Régis; Mallet, Vincent

Beyond Trikafta: new models to assess tissue dependent rescue of N1303K-CFTR

Trikafta 之外:评估 N1303K-CFTR 组织依赖性拯救的新模型

Pranke, Iwona; Capurro, Valeria; Chevalier, Benoit; Pesce, Emanuela; Tomati, Valeria; Pastorino, Cristina; Kelly-Aubert, Mairead; Hatton, Aurelie; Dreano, Elise; Lena, Mariateresa; Bocciardi, Renata; Zara, Federico; Pantano, Stefano; Terlizzi, Vito; Lucanto, Cristina; Costa, Stefano; Claut, Laura; Daccò, Valeria; Poli, Piercarlo; Maschio, Massimo; Fabrizzi, Benedetta; Caporelli, Nicole; Cipolli, Marco; Volpi, Sonia; Chedevergne, Frederique; Cosson, Laure; Macey, Julie; Ramel, Sophie; Weiss, Laurence; Grenet, Dominique; Le Clainche-Viala, Laurence; Douvry, Benoit; Ravoninjatovo, Bruno; Audousset, Camille; Tatopoulos, Aurélie; Richaud-Thiriez, Bénédicte; Baravalle, Melissa; Thouvenin, Guillaume; Labbé, Guillaume; Mittaine, Marie; Reix, Philippe; Durieu, Isabelle; Mankikian, Julie; Bui, Stéphanie; Nguyen-Khoa, Thao; Khoukh, Karim; Martin, Clémence; Da Silva, Jennifer; De Carli, Paola; Castellani, Carlo; Cresta, Federico; Galietta, Luis; Guillemaut, Anne; Girodon, Emmanuelle; Remus, Natacha; Bulcaen, Mathis; Ensinck, Marjolein; Zajac, Miroslaw; Carlon, Marianne; LeBihan, Jean; Burgel, Pierre-Régis; Sermet-Gaudelus, Isabelle; Hinzpeter, Alexandre; Pedemonte, Nicoletta

Neutrophils Display Novel Partners of Cytosolic Proliferating Cell Nuclear Antigen Involved in Interferon Response in COVID-19 Patients

中性粒细胞显示胞质增殖细胞核抗原的新伙伴参与COVID-19患者的干扰素反应

Lucie Pesenti,Rodrigo de Oliveira Formiga,Nicola Tamassia,Elisa Gardiman,François Chable de La Héronnière,Sara Gasperini,Johana Chicher,Lauriane Kuhn,Philippe Hammann,Morgane Le Gall,Giovanni Saraceni-Tasso,Clémence Martin,Anne Hosmalin,Magali Breckler,Roxane Hervé,Patrice Decker,Maha Zohra Ladjemi,Frédéric Pène,Pierre-Régis Burgel,Marco A Cassatella,Véronique Witko-Sarsat

Efficacy and safety of CFTR modulators in patients with interstitial lung disease caused by ABCA3 transporter deficiency

CFTR调节剂治疗ABCA3转运蛋白缺乏引起的间质性肺病患者的疗效和安全性

Le Brun, Mathilde; Nathan, Nadia; Louvrier, Camille; Legendre, Marie; Feuillet, Severine; Frija-Masson, Justine; Onanga, Mwetty; Morer, Lise; Debray, Marie-Pierre; Fajac, Isabelle; Burgel, Pierre-Régis; Marchand-Adam, Sylvain; Crestani, Bruno; Borie, Raphaël