Long-term safety of dexamethasone sodium phosphate encapsulated in autologous erythrocytes in pediatric patients with ataxia telangiectasia
自体红细胞包裹的磷酸地塞米松钠在毛细血管扩张性共济失调患儿中的长期安全性
期刊:Frontiers in Neurology
影响因子:2.8
doi:10.3389/fneur.2024.1526914
Koenig, Mary Kay; Leuzzi, Vincenzo; Gouider, Riadh; Yiu, Eppie M; Pietrucha, Barbara; Stray-Pedersen, Asbjørg; Perlman, Susan L; Wu, Steve; Burgers, Trudy; Borgohain, Rupam; Kandadai, Rukmini Mridula; Meyts, Isabelle; Bucciol, Giorgia; Udwadia-Hegde, Anaita; Yadav, Ravi; Roberts, Donna; Dane, Aaron; Roden, Maureen; Thye, Dirk; Horn, Biljana; Lederman, Howard M; Whitehouse, William P