日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

LncRNA-splicing factor condensates regulate hypoxia-responsive pre-mRNA processing near nuclear speckles.

LncRNA剪接因子凝聚体调节核斑点附近的缺氧反应前体mRNA加工。

Song You Jin, Shinn Min Kyung, Bangru Sushant, Wang Yu, Sun Qinyu, Hao Qinyu, Chaturvedi Pankaj, Freier Susan M, Perez-Pinera Pablo, Nelson Erik R, Belmont Andrew S, Guttman Mitchell, Prasanth Supriya G, Kalsotra Auinash, Pappu Rohit V, Prasanth Kannanganattu V

Systemic administration of an RNA binding and cell-penetrating antibody targets therapeutic RNA to multiple mouse models of cancer.

系统性地施用一种 RNA 结合和细胞穿透抗体,将治疗性 RNA 靶向应用于多种小鼠癌症模型

Quijano Elias, Martinez-Saucedo Diana, Ianniello Zaira, Pinto-Medici Natasha, Rackear Madison, Chen Haoting, Lola-Pereira Luiz, Liu Yanfeng, Hegan Denise, Shan Xinning, Tseng Robert, Yugawa Deanne, Chowdhury Sumedha, Khang Minsoo, Singh Jay P, Abdullah Rashed, Azhir Perisa, Kashima Soki, Woods Wendy S, Gosstola Nicholas, Turner Bruce C, Squinto Stephen, Ludwig Dale L, Bindra Ranjit S, Robert Marie E, Braun David A, Perez Pinera Pablo, Saltzman W Mark, Escobar-Hoyos Luisa F, Glazer Peter M

Incidental Discovery of Dystrophic Myocardial Calcification

偶然发现营养不良性心肌钙化

Ramos-Cázares, Ray Erick; Rivera-Florez, Juan Sebastián; Pedraza-Jiménez, Rafael; Vera-Pinera, Raymundo; Mascorro-Cienfuegos, César Alejandro; Ordaz-Farias, Alejandro; Urrutia-Stamatio, Bernardo; Flores-Ramírez, Ramiro; Carrizales-Sepúlveda, Edgar Francisco; Uresti, Osvaldo

Corrigendum: Chromatin structure and context-dependent sequence features control prime editing efficiency

更正:染色质结构和上下文依赖性序列特征控制着主要编辑效率

Kim, Somang; Yuan, Jimmy B; Woods, Wendy S; Newton, Destry A; Perez-Pinera, Pablo; Song, Jun S

A genome-wide cytotoxicity screen of cluster F1 mycobacteriophage Girr reveals novel inhibitors of Mycobacterium smegmatis growth

对F1簇分枝杆菌噬菌体Girr进行全基因组细胞毒性筛选,揭示了耻垢分枝杆菌生长的新型抑制剂。

Pollenz, Richard S; Barnhill, Kaylee; Biggs, Abbigail; Bland, Jackson; Carter, Victoria; Chase, Michael; Clark, Hayley; Coleman, Caitlyn; Daffner, Marshall; Deam, Caitlyn; Finocchiaro, Alyssa; Franco, Vanessa; Fuller, Thomas; Pinera, Juan Gallardo; Horne, Mae; Howard, Zoe; Kanahan, Olivia; Miklaszewski, Christopher; Miller, Sydney; Morgan, Ryan; Onalaja, Oluwatobi; Otero, Louis; Padhye, Shivani; Rainey, Emily; Rasul, Fareed; Robichaux, Kobe; Rodier, Alexandra; Schlosser, Sydni; Sciacchitano, Ava; Stewart, Emma; Thakkar, Rajvi; Heller, Danielle M

Chromatin-associated lncRNA-splicing factor condensates regulate hypoxia responsive RNA processing of genes pre-positioned near nuclear speckles

染色质相关lncRNA剪接因子凝聚体调节位于核斑点附近的基因的缺氧响应性RNA加工

Song, You Jin; Shinn, Min Kyung; Bangru, Sushant; Wang, Yu; Sun, Qinyu; Hao, Qinyu; Chaturvedi, Pankaj; Freier, Susan M; Perez-Pinera, Pablo; Nelson, Erik R; Belmont, Andrew S; Guttman, Mitchell; Prasanth, Supriya G; Kalsotra, Auinash; Pappu, Rohit V; Prasanth, Kannanganattu V

SPLICER: A Highly Efficient Base Editing Toolbox That Enables In Vivo Therapeutic Exon Skipping

SPLICER:一种高效的碱基编辑工具箱,可实现体内治疗性外显子跳跃

Miskalis, Angelo; Shirguppe, Shraddha; Winter, Jackson; Elias, Gianna; Swami, Devyani; Nambiar, Ananthan; Stilger, Michelle; Woods, Wendy S; Gosstola, Nicholas; Gapinske, Michael; Zeballos, Alejandra; Moore, Hayden; Maslov, Sergei; Gaj, Thomas; Perez-Pinera, Pablo

Targeting Duchenne muscular dystrophy by skipping DMD exon 45 with base editors

使用碱基编辑器跳过 DMD 外显子 45 来治疗杜氏肌营养不良症

Michael Gapinske, Jackson Winter, Devyani Swami, Lauren Gapinske, Wendy S Woods, Shraddha Shirguppe, Angelo Miskalis, Anna Busza, Dana Joulani, Collin J Kao, Kurt Kostan, Anne Bigot, Rashid Bashir, Pablo Perez-Pinera

Protein Engineering Technologies for Development of Next-Generation Genome Editors

用于开发下一代基因组编辑器的蛋白质工程技术

Winter, Jackson; Shirguppe, Shraddha; Perez-Pinera, Pablo

CRISPR base editing of cis-regulatory elements enables the perturbation of neurodegeneration-linked genes

CRISPR 碱基编辑顺式调控元件能够扰动与神经退行性疾病相关的基因

Colin K W Lim, Tristan X McCallister, Christian Saporito-Magriña, Garrett D McPheron, Ramya Krishnan, M Alejandra Zeballos C, Jackson E Powell, Lindsay V Clark, Pablo Perez-Pinera, Thomas Gaj