Base editing effectively prevents early-onset severe cardiomyopathy in Mybpc3 mutant mice
碱基编辑可有效预防Mybpc3突变小鼠早期发生严重心肌病。
期刊:Cell Research
影响因子:25.9
doi:10.1038/s41422-024-00930-7
Wu, Shuo; Yang, Ping; Geng, Zilong; Li, Yige; Guo, Zhizhao; Lou, Yingmei; Zhang, Shasha; Xiong, Junhao; Hu, Huan; Guo, Xiaoling; Pu, William T; Zhang, Yan; Zhu, Dan; Zhang, Bing