日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Etranacogene dezaparvovec in people with hemophilia B with preexisting adeno-associated virus 5 neutralizing antibodies: 4-year subgroup results from the HOPE-B trial

在伴有预先存在的腺相关病毒5型中和抗体的B型血友病患者中应用依曲那康基因(Etranacogene dezaparvovec):HOPE-B试验的4年亚组结果

Klamroth, Robert; Monahan, Paul E; Van der Valk, Paul; Quon, Doris; Kazmi, Rashid Saeed; Coppens, Michiel; O'Connell, Niamh; Pipe, Steven W; von Drygalski, Annette; Afzal, Saira; Gabriel, Richard; Youssar, Loubna; Gill, Sean; Jansen, Nathalie; Wang, Fei; Le Quellec, Sandra; Hermans, Cedric

Efficacy of prophylactic dosing of diclazuril for the prevention of coccidiosis in captive-reared North Island brown kiwi (Apteryx mantelli) chicks

预防性使用地克珠利治疗圈养北岛褐奇异鸟(Apteryx mantelli)雏鸟球虫病的疗效

Scheltema, Emma; Singh, Preet; Howe, Laryssa; Godfrey, A Jonathan R; Wilkinson, Bev; Pipe, Veronika; Morgan, Kerri

Protocol for the precise activation of intradental neurons in mice via electrical stimulation

通过电刺激精确激活小鼠牙槽内神经元的方案

Wan, Shuhao; Ronan, Elizabeth A; Jha, Aditi; Gandhi, Akash R; Constantinescu, Brian S C; Pipe, Kevin P; Emrick, Joshua J

Safety and efficacy of a fitusiran antithrombin-based dose regimen in people with hemophilia A or B: the ATLAS-OLE study

在A型或B型血友病患者中,基于fitusiran抗凝血酶的给药方案的安全性和有效性:ATLAS-OLE研究

Young, Guy; Kavakli, Kaan; Klamroth, Robert; Matsushita, Tadashi; Peyvandi, Flora; Pipe, Steven W; Rangarajan, Savita; Shen, Ming-Ching; Srivastava, Alok; Sun, Jing; Tran, Huyen; You, Chur-Woo; Zülfikar, Bülent; Menapace, Laurel A; Zhang, Chuanwu; Shen, Yuqian; Puurunen, Marja; Demissie, Marek; Kenet, Gili

A dedicated skin-to-brain circuit for cool sensation in mice.

小鼠体内一条专门用于感知凉爽的皮肤到大脑的回路

Lee Hankyu, Hor Chia Chun, Horwitz Lorraine R, Xiong Ailin, Su Xin-Yu, Soden Daniel R, Yang Sarah, Cai Wei, Zhang Wenwen, Li Chen, Radcliff Christopher, Dinh Abbey, Fung Tin Long Rex, Rovcanin Ilma, Pipe Kevin P, Xu X Z Shawn, Duan Bo

Clinical perspective: Advancing hemophilia treatment through gene therapy approaches

临床视角:通过基因治疗方法推进血友病治疗

Thornburg, Courtney D; Pipe, Steve W; Cantore, Alessio; Unzu, Carmen; Jones, Micheala; Miesbach, Wolfgang A

Intradental mechano-nociceptors serve as sentinels that prevent tooth damage

牙内机械伤害感受器如同哨兵一般,能够防止牙齿损伤。

Elizabeth A Ronan ,Akash R Gandhi ,Karin H Uchima Koecklin ,Yujia Hu ,Shuhao Wan ,Brian S C Constantinescu ,Mak E Guenther ,Maximilian Nagel ,Ling-Yu Liu ,Aditi Jha ,Leen Dakhilalla ,Kaitlyn J Blumberg ,Isaac T Berthaume ,Tomer Stern ,Kevin P Pipe ,Bing Ye ,Peng Li ,Joshua J Emrick

Gene therapy for hemophilia B: results from the phase 1/2 101HEMB01/02 studies

B型血友病基因疗法:101HEMB01/02 1/2期研究结果

Pipe, Steven; Poma, Allen; Rajasekhar, Anita; Everington, Tamara; Sankoh, Serap; Allen, Jack; Cataldo, Jason; Crombez, Eric

Long-term safety and efficacy of fitusiran prophylaxis, and perioperative management, in people with hemophilia A or B

菲图西兰预防性治疗及围手术期管理在A型或B型血友病患者中的长期安全性和有效性

Pipe, Steven W; Lissitchkov, Toshko; Georgiev, Pencho; Mangles, Sarah; Hegemann, Inga; Trinchero, Alice; Chowdary, Pratima; Forbes, Adam; Feng, Liqi; Menapace, Laurel A; Kichou, Salim; Andersson, Shauna; Demissie, Marek; Ragni, Margaret V

Completion of phase 2b trial of etranacogene dezaparvovec gene therapy in patients with hemophilia B over 5 years

针对B型血友病患者的etranacogene dezaparvovec基因疗法的2b期试验已完成5年

von Drygalski, Annette; Gomez, Esteban; Giermasz, Adam; Castaman, Giancarlo; Key, Nigel S; Lattimore, Susan U; Leebeek, Frank W G; Miesbach, Wolfgang A; Recht, Michael; Monahan, Paul E; Le Quellec, Sandra; Pipe, Steven W