日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

A metabolite-based resistance mechanism against malaria

一种基于代谢物的抗疟疾机制

Figueiredo, Ana; Rastogi, Sonia Trikha; Ramos, Susana; Nogueira, Fátima; De Villiers, Katherine; de Sousa, António G Gonçalves; Votborg-Novél, Lasse; von Wedel, Cäcilie; Tober-Lau, Pinkus; Jentho, Elisa; Pagnotta, Sara; Mesquita, Miguel; Cardoso, Silvia; Bortolussi, Giulia; Muro, Andrés F; Tranfield, Erin M; Thibaud, Jessica; Duarte, Denise; Sousa, Ana Laura; Pinto, Sandra N; Kitoko, Jamil; Mombo-Ngoma, Ghyslain; Mischlinger, Johannes; Junttila, Sini; Alenquer, Marta; Amorim, Maria João; Vasavda, Chirag; Bosma, Piter J; Violante, Sara; Drotleff, Bernhard; Paixão, Tiago; Portugal, Silvia; Kurth, Florian; Elo, Laura L; Paul, Bindu D; Martins, Rui; Soares, Miguel P

The Phospholipid Flippase ATP8B1 is Involved in the Pathogenesis of Ulcerative Colitis via Establishment of Intestinal Barrier Function

磷脂翻转酶ATP8B1通过建立肠道屏障功能参与溃疡性结肠炎的发病机制。

Pim J Koelink ,Valentina E Gómez-Mellado ,Suzanne Duijst ,Manon van Roest ,Sander Meisner ,Kam S Ho-Mok ,Sabrina Frank ,Babette S Appelman ,Lysbeth Ten Bloemendaal ,Georg F Vogel ,Stan F J van de Graaf ,Piter J Bosma ,Ronald P J Oude Elferink ,Manon E Wildenberg ,Coen C Paulusma

Gene Therapy for Inherited Liver Disease: To Add or to Edit

遗传性肝病的基因疗法:添加或编辑

Chen, Yue; van Til, Niek P; Bosma, Piter J

Long-Term Effects of Biliverdin Reductase a Deficiency in Ugt1-/- Mice: Impact on Redox Status and Metabolism

Ugt1-/- 小鼠胆绿素还原酶 a 缺乏的长期影响:对氧化还原状态和代谢的影响

Giulia Bortolussi, Xiaoxia Shi, Lysbeth Ten Bloemendaal, Bhaswati Banerjee, Dirk R De Waart, Gabriele Baj, Weiyu Chen, Ronald P Oude Elferink, Ulrich Beuers, Coen C Paulusma, Roland Stocker, Andrés F Muro, Piter J Bosma

Gene Therapy for Progressive Familial Intrahepatic Cholestasis: Current Progress and Future Prospects

基因疗法治疗进行性家族性肝内胆汁淤积症:当前进展与未来展望

Bosma, Piter J; Wits, Marius; Oude-Elferink, Ronald Pj

A Quantitative In Vitro Potency Assay for Adeno-Associated Virus Vectors Encoding for the UGT1A1 Transgene

编码 UGT1A1 转基因的腺相关病毒载体的体外定量效力测定

Sem J Aronson, Robert S Bakker, Sascha Moenis, Remco van Dijk, Giulia Bortolussi, Fanny Collaud, Xiaoxia Shi, Suzanne Duijst, Lysbeth Ten Bloemendaal, Giuseppe Ronzitti, Andrés F Muro, Federico Mingozzi, Ulrich Beuers, Piter J Bosma

Efficacy of AAV8-h UGT1A1 with Rapamycin in neonatal, suckling, and juvenile rats to model treatment in pediatric CNs patients

AAV8-h UGT1A1 与雷帕霉素对新生大鼠、哺乳大鼠和幼年大鼠的疗效,可作为儿童 CNs 患者治疗的模型

Xiaoxia Shi, Sem J Aronson, Lysbeth Ten Bloemendaal, Suzanne Duijst, Robert S Bakker, Dirk R de Waart, Giulia Bortolussi, Fanny Collaud, Ronald P Oude Elferink, Andrés F Muro, Federico Mingozzi, Giuseppe Ronzitti, Piter J Bosma

Prevalence and Relevance of Pre-Existing Anti-Adeno-Associated Virus Immunity in the Context of Gene Therapy for Crigler-Najjar Syndrome

在克里格勒-纳贾尔综合征基因治疗背景下预先存在的抗腺相关病毒免疫的流行率和相关性

Sem J Aronson, Philippe Veron, Fanny Collaud, Aurélie Hubert, Virginie Delahais, Géraldine Honnet, Robert J de Knegt, Norman Junge, Ulrich Baumann, Angelo Di Giorgio, Lorenzo D'Antiga, Virginia M Ginocchio, Nicola Brunetti-Pierri, Philippe Labrune, Ulrich Beuers, Piter J Bosma, Federico Mingozzi

The P4-ATPase ATP9A is a novel determinant of exosome release

P4-ATPase ATP9A 是外泌体释放的新决定因素

Jyoti Naik, Chi M Hau, Lysbeth Ten Bloemendaal, Kam S Mok, Najat Hajji, Ann M Wehman, Sander Meisner, Vanesa Muncan, Nanne J Paauw, H E de Vries, Rienk Nieuwland, Coen C Paulusma, Piter J Bosma

A novel UGT1A1 gene mutation causing severe unconjugated hyperbilirubinemia: a case report

一种新型UGT1A1基因突变导致严重非结合型高胆红素血症:病例报告

Shi, Xiaoxia; Aronson, Sem; Khan, Ahmed Sharif; Bosma, Piter J