Artificial enforcement of the unfolded protein response reduces disease features in multiple preclinical models of ALS/FTD.
人工诱导未折叠蛋白反应可减少 ALS/FTD 多个临床前模型中的疾病特征
期刊:Molecular Therapy
影响因子:12
doi:10.1016/j.ymthe.2025.01.004
Valenzuela Vicente, Becerra Daniela, Astorga José I, Fuentealba MatÃas, Diaz Guillermo, Bargsted Leslie, Chacón Carlos, Martinez Alexis, Gozalvo Romina, Jackson Kasey, Morales Vania, Heras Macarena Las, Tamburini Giovanni, Petrucelli Leonard, Sardi S Pablo, Plate Lars, Hetz Claudio