日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

CCND3 Suppression Ameliorates β-Thalassaemia in a Murine Disease Model: A Potential Therapeutic Strategy

CCND3抑制可改善小鼠疾病模型中的β-地中海贫血:一种潜在的治疗策略

Caria, Cristian Antonio; Marongiu, Maria Franca; Porcu, Susanna; Poddie, Daniela; Vaccargiu, Simona; Vadolas, Jim; Meloni, Alessandra; Perseu, Lucia; Olianas, Alessandra; Ristaldi, Maria Serafina

Drugs Repurposing of Molecules Modulating Human Delta Globin Gene Expression via a Model of Transgenic Foetal Liver Cells: Implications for Beta-Hemoglobinopathy Therapeutics.

通过转基因胎肝细胞模型对调节人类δ珠蛋白基因表达的分子进行药物再利用:对β-血红蛋白病治疗的意义

Simbula Michela, Manchinu Maria Francesca, Olla Stefania, Congiu Michela, Vaccargiu Simona, Caria Cristian Antonio, Poddie Daniela, Ristaldi Maria Serafina

Post-GWAS Validation of Target Genes Associated with HbF and HbA(2) Levels

GWAS后验证与HbF和HbA(2)水平相关的靶基因

Caria, Cristian Antonio; Faà, Valeria; Porcu, Susanna; Marongiu, Maria Franca; Poddie, Daniela; Perseu, Lucia; Meloni, Alessandra; Vaccargiu, Simona; Ristaldi, Maria Serafina

In vivo activation of the human δ-globin gene: the therapeutic potential in β-thalassemic mice

人δ-珠蛋白基因的体内激活:在β-地中海贫血小鼠中的治疗潜力

Manchinu, Maria F; Marongiu, Maria F; Poddie, Daniela; Casu, Carla; Latini, Veronica; Simbula, Michela; Galanello, Renzo; Moi, Paolo; Cao, Antonio; Porcu, Susanna; Ristaldi, Maria S

Reversible disruption of pre-pulse inhibition in hypomorphic-inducible and reversible CB1-/- mice

在低效诱导型和可逆型 CB1-/- 小鼠中,预脉冲抑制的可逆性破坏

Marongiu, Maria Franca; Poddie, Daniela; Porcu, Susanna; Manchinu, Maria Francesca; Castelli, Maria Paola; Sogos, Valeria; Bini, Valentina; Frau, Roberto; Caredda, Elisabetta; Collu, Maria; Ristaldi, Maria Serafina