PABPN1 gene therapy for oculopharyngeal muscular dystrophy
PABPN1基因治疗眼咽型肌营养不良症
期刊:Nature Communications
影响因子:14.7
doi:10.1038/ncomms14848
A Malerba, P Klein, H Bachtarzi, S A Jarmin, G Cordova, A Ferry, V Strings, M Polay Espinoza, K Mamchaoui, S C Blumen, J Lacau St Guily, V Mouly, M Graham, G Butler-Browne, D A Suhy, C Trollet, G Dickson