In vivo KCNQ1-suppression-replacement gene therapy in transgenic rabbits with type 1 long QT syndrome
在患有1型长QT综合征的转基因兔中进行体内KCNQ1抑制替代基因治疗
期刊:Cerebral Cortex
影响因子:2.9
doi:10.1093/cercor/bhac535
Globig, Laura K; Gianotti, Lorena R R; Ponsi, Giorgia; Koenig, Thomas; Dahinden, Franziska M; Knoch, Daria; Kueffer, T; Madaffari, A; Muehl, A; Maurhofer, J; Stefenova, A; Seiler, J; Thalmann, G; Kozhuharov, N A; Servatius, H; Tanner, H; Haeberlin, A; Baldinger, S H; Noti, F; Roten, L; Reichlin, T; Luker, J; Strik, M; Andrade, J G; Raymond Paquin, A; Elrefai, M H; Cano Perez, O; Kron, J; Schmitt, J; Pott, A; Veltmann, C; Srinivasan, N T; Van Stipdonk, A; Fluschnik, N; Haeberlin, A; Steven, D; Hennings, E; Bhend, K; Paladini, R E; Aeschbacher, S; Coslovsky, M; Rodondi, N; Beer, J H; Auricchio, A; Moschovitis, G; Chocano, P; Sinnecker, T; Conen, D; Kuehne, M; Bonati, L H; Osswald, S; Luca, A; Coudray, E; Vesin, J M; Le Bloa, M; Teres, C; Herrera, C; Roten, L; Kuehne, M; Spies, F; Knecht, S; Sticherling, C; Pascale, P; Pruvot, E; Kueffer, T; Madaffari, A; Muehl, A; Seiler, J; Thalmann, G; Servatius, H; Kozhuharov, N A; Tanner, H; Haeberlin, A; Noti, A; Baldinger, S H; Roten, L; Reichlin, T; Hödl, Tatjana; Myrach, Thomas; Kueffer, T; Madaffari, A; Muehl, A; Maurhofer, J; Stefenova, A; Seiler, J; Thalmann, G; Kozhuharov, N A; Servatius, H; Tanner, H; Haeberlin, A; Baldinger, S H; Noti, F; Roten, L; Reichlin, T; Kueffer, T; Madaffari, A; Muehl, A; Seiler, J; Thalmann, G; Servatius, H; Tanner, H; Haeberlin, A; Baldinger, S H; Kozhuharov, N A; Noti, F; Reichlin, T; Roten, L; Prudat, Y; Luca, A; Derval, N; Jais, P; Roten, L; Kobza, R; Berte, B; Le Bloa, M; Herrera-Siklody, C; Teres, C; Pruvot, E; Vesin, J M; Pascale, P; Garweg, C; Breitenstein, A; Brock Johansen, J; Clementy, N; De Asmundis, C; Iacopino, S; Sharman, D; Theis, C; Vinolas, X; Winter, S; Reichlin, T; Giammarino, L; Nimani, S; Bains, S; Alerni, N; Tester, D J; Christoforou, N; Louradour, J; Jurgensen, J; Barry, M A; Koren, G; Zehender, M; Brunner, M; Brooks, G; Ackerman, M J; Odening, K E