Base editing of key residues in the BCL11A-XL-specific zinc finger domains derepresses fetal globin expression
BCL11A-XL特异性锌指结构域关键残基的碱基编辑可解除胎儿珠蛋白表达的抑制。
期刊:Molecular Therapy
影响因子:12
doi:10.1016/j.ymthe.2024.01.023
Rajendiran, Vignesh; Devaraju, Nivedhitha; Haddad, Mahdi; Ravi, Nithin Sam; Panigrahi, Lokesh; Paul, Joshua; Gopalakrishnan, Chandrasekar; Wyman, Stacia; Ariudainambi, Keerthiga; Mahalingam, Gokulnath; Periyasami, Yogapriya; Prasad, Kirti; George, Anila; Sukumaran, Dhiyaneshwaran; Gopinathan, Sandhiya; Pai, Aswin Anand; Nakamura, Yukio; Balasubramanian, Poonkuzhali; Ramalingam, Rajasekaran; Thangavel, Saravanabhavan; Velayudhan, Shaji R; Corn, Jacon E; Mackay, Joel P; Marepally, Srujan; Srivastava, Alok; Crossley, Merlin; Mohankumar, Kumarasamypet M