日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Transgene-induced cardiotoxicity in high-dose AAV gene transfer

高剂量AAV基因转移中转基因诱导的心脏毒性

Biquand, Ariane; Gicquel, Evelyne; Poupiot, Jerome; Faivre, Marine; Campuzano, Stephany; Bourgeton, Tiffany; Le Brun, Pierre-Romain; Veron, Philippe; Brureau, Anthony; Richard, Isabelle

Lysosomal damage is a therapeutic target in Duchenne muscular dystrophy

溶酶体损伤是杜氏肌营养不良症的治疗靶点。

Jaber, Abbass; Palmieri, Laura; Bakour, Rania; Bourg, Nathalie; Hong, Ai Vu; Lachiver, Elise; Roudaut, Carinne; Poupiot, Jérôme; Albini, Sonia; Stockholm, Daniel; Van Wittenberghe, Laetitia; Miranda, Adeline; Tanniou, Guillaume; Danièle, Nathalie; Barthélémy, Inès; Blot, Stephane; Bui, Mai Thao; Das, Bornale; Malfatti, Edoardo; Evangelista, Teresinha; Richard, Isabelle; Israeli, David

An engineered AAV targeting integrin alpha V beta 6 presents improved myotropism across species

针对整合素 alpha V beta 6 的工程化 AAV 可在各个物种中表现出更好的肌向性

Ai Vu Hong #, Laurence Suel #, Eva Petat, Auriane Dubois, Pierre-Romain Le Brun, Nicolas Guerchet, Philippe Veron, Jérôme Poupiot, Isabelle Richard

Dlk1-Dio3 cluster miRNAs regulate mitochondrial functions in the dystrophic muscle in Duchenne muscular dystrophy

Dlk1-Dio3 簇 miRNA 调节杜氏肌营养不良症患者营养不良肌肉中的线粒体功能

Ai Vu Hong, Nathalie Bourg, Peggy Sanatine, Jerome Poupiot, Karine Charton, Evelyne Gicquel, Emmanuelle Massourides, Marco Spinazzi, Isabelle Richard, David Israeli

Role of Regulatory T Cell and Effector T Cell Exhaustion in Liver-Mediated Transgene Tolerance in Muscle

调节性 T 细胞和效应性 T 细胞耗竭在肝脏介导的肌肉转基因耐受中的作用

Jérôme Poupiot, Helena Costa Verdera, Romain Hardet, Pasqualina Colella, Fanny Collaud, Laurent Bartolo, Jean Davoust, Peggy Sanatine, Federico Mingozzi, Isabelle Richard, Giuseppe Ronzitti

Temporary Reduction of Membrane CD4 with the Antioxidant MnTBAP Is Sufficient to Prevent Immune Responses Induced by Gene Transfer

使用抗氧化剂 MnTBAP 暂时减少膜 CD4 足以预防基因转移引起的免疫反应

Sylvie Da Rocha, Jérémy Bigot, Fanny Onodi, Jérémie Cosette, Guillaume Corre, Jérôme Poupiot, David Fenard, Bernard Gjata, Anne Galy, Thi My Anh Neildez-Nguyen

An AAV-SGCG Dose-Response Study in a γ-Sarcoglycanopathy Mouse Model in the Context of Mechanical Stress

在机械应力背景下对 γ-肌聚糖病小鼠模型进行 AAV-SGCG 剂量反应研究

David Israeli, Jérémie Cosette, Guillaume Corre, Fatima Amor, Jérôme Poupiot, Daniel Stockholm, Marie Montus, Bernard Gjata, Isabelle Richard

Circulating miRNAs are generic and versatile therapeutic monitoring biomarkers in muscular dystrophies

循环miRNA是肌营养不良症中通用且用途广泛的治疗监测生物标志物。

Israeli, David; Poupiot, Jérôme; Amor, Fatima; Charton, Karine; Lostal, William; Jeanson-Leh, Laurence; Richard, Isabelle

Serum proteomic profiling reveals fragments of MYOM3 as potential biomarkers for monitoring the outcome of therapeutic interventions in muscular dystrophies

血清蛋白质组学分析显示 MYOM3 片段可作为监测肌营养不良症治疗干预结果的潜在生物标志物

Jérémy Rouillon, Jérôme Poupiot, Aleksandar Zocevic, Fatima Amor, Thibaut Léger, Camille Garcia, Jean-Michel Camadro, Brenda Wong, Robin Pinilla, Jérémie Cosette, Anna M L Coenen-Stass, Graham Mcclorey, Thomas C Roberts, Matthew J A Wood, Laurent Servais, Bjarne Udd, Thomas Voit, Isabelle Richard, F

Rescue of sarcoglycan mutations by inhibition of endoplasmic reticulum quality control is associated with minimal structural modifications

通过抑制内质网质量控制来挽救肌聚糖突变与最小的结构修改有关

Tayebeh Soheili, Evelyne Gicquel, Jérôme Poupiot, Luu N'Guyen, Florence Le Roy, Marc Bartoli, Isabelle Richard