日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Clinical applications of induced pluripotent stem cell-mediated therapies in cancer: progress, challenges, and future directions

诱导多能干细胞介导疗法在癌症治疗中的临床应用:进展、挑战和未来方向

AlKhafaje, Zahraa; Malathi, H; Dash, Aniruddh; Precilla, Selvakumari J; Singh, Gurjant; Sinha, Aashna; Suliman, Muath; Smerat, Aseel

Differential tractography: an imaging marker for tissue degeneration in neurodegenerative diseases

差异性纤维束成像:神经退行性疾病中组织退化的影像学标志物

Lewis, Connor J; Vardar, Zeynep; Kühn, Anna Luisa; Johnston, Jean M; D'Souza, Precilla; Yousef, Muhammad H; Gahl, William A; Shazeeb, Mohammed Salman; Tifft, Cynthia J; Acosta, Maria T

Anti-tumor efficacy and safety of AEV01 in preclinical glioblastoma and hepatocellular carcinoma models

AEV01在临床前胶质母细胞瘤和肝细胞癌模型中的抗肿瘤疗效和安全性

Biswas, Indrani; Precilla, Senthilathiban Daisy; Kumar, Aravinda; Sekhar, M M; Medasani, Renu; Anitha, T S

Corrigendum to "Natural history progression of MRI brain volumetrics in type II late-infantile and juvenile GM1 gangliosidosis patients" [Molecular Genetics and Metabolism 2025 Mar;144(3):109025]

对“II 型晚期婴儿和青少年 GM1 神经节苷脂病患者的 MRI 脑体积自然史进展”的更正 [分子遗传学和代谢 2025 年 3 月;144(3):109025]

Kolstad, Josephine; Zoppo, Christopher; Johnston, Jean M; D'Souza, Precilla; Kühn, Anna Luisa; Vardar, Zeynep; Peker, Ahmet; Hader, Asma; Celik, Hakki; Lewis, Connor J; Lindsay, Clifford; Rentiya, Zubir S; Lebel, Catherine; Vedantham, Srinivasan; Vachha, Behroze; Gray-Edwards, Heather L; Acosta, Maria T; Tifft, Cynthia J; Shazeeb, Mohammed Salman

Natural history progression of MRI brain volumetrics in type II late-infantile and juvenile GM1 gangliosidosis patients

II型晚期婴儿期和青少年期GM1神经节苷脂沉积症患者的MRI脑容量自然史进展

Kolstad, Josephine; Zoppo, Christopher; Johnston, Jean M; D'Souza, Precilla; Kühn, Anna Luisa; Vardar, Zeynep; Peker, Ahmet; Hader, Asma; Celik, Hakki; Lewis, Connor J; Lindsay, Clifford; Rentiya, Zubir S; Lebel, Catherine; Vedantham, Srinivasan; Vachha, Behroze; Gray-Edwards, Heather L; Acosta, Maria T; Tifft, Cynthia J; Shazeeb, Mohammed Salman

Retrospective assessment of clinical global impression of severity and change in GM1 gangliosidosis: a tool to score natural history data in rare disease cohorts

回顾性评估GM1神经节苷脂沉积症的临床总体印象严重程度和变化:一种用于对罕见病队列的自然史数据进行评分的工具

Lewis, Connor J; Johnston, Jean M; Zaragoza Domingo, Silvia; Vezina, Gilbert; D'Souza, Precilla; Gahl, William A; Adams, David A; Tifft, Cynthia J; Acosta, Maria T

Brain morphometry of toddlers with language delay: An exploratory study

语言发育迟缓幼儿脑形态测量:一项探索性研究

Filippi, Courtney A; Smith, Elizabeth; Redcay, Elizabeth; Hazlett, Heather; Thompson, Lauren; Manwaring, Stacy S; D'Souza, Precilla; Thurm, Audrey

A Case for Automated Segmentation of MRI Data in Neurodegenerative Diseases: Type II GM1 Gangliosidosis

神经退行性疾病中MRI数据自动分割的必要性:以II型GM1神经节苷脂病为例

Lewis, Connor J; Johnston, Jean M; D'Souza, Precilla; Kolstad, Josephine; Zoppo, Christopher; Vardar, Zeynep; Kühn, Anna Luisa; Peker, Ahmet; Rentiya, Zubir S; Yousef, Muhammad H; Gahl, William A; Shazeeb, Mohammed Salman; Tifft, Cynthia J; Acosta, Maria T

AAV9 Gene Therapy in GM1 Gangliosidosis Type II: A Phase 1/2 Trial

AAV9基因疗法治疗GM1神经节苷脂沉积症II型:一项1/2期临床试验

Lewis, Connor J; D'Souza, Precilla; Johnston, Jean M; Acosta, Maria T; Farmer, Cristan; Baker, Eva H; Crowell, Anna; Mojica, Yoliann; Rahman, Sumaiya; Joseph, Lisa; Hartman, Adam; Vézina, Gilbert; Quezado, Zenaide; Yousef, Muhammad H; Luckett, Amelia; Vardar, Zeynep; Shazeeb, Mohammad Salman; Corti, Manuela; Blackwood, Meghan; Coleman, Kirsten; Thurm, Audrey; De Boever, Erika; Gahl, William A; Byrne, Barry J; Flotte, Terence R; Jiang, Xuntian; Gross, Amanda L; Keeler, Allison M; Gray-Edwards, Heather; Martin, Douglas R; Sena-Esteves, Miguel; Tifft, Cynthia J

Brain Age Prediction in Type II GM1 Gangliosidosis

II型GM1神经节苷脂病患者的脑龄预测

Lewis, Connor J; Chipman, Selby I; D'Souza, Precilla; Johnston, Jean M; Yousef, Muhammad H; Gahl, William A; Tifft, Cynthia J; Acosta, Maria T