日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Can Alpha-Glucosidase Activity in Plasma or Leukocytes Serve as a Biomarker for Future Gene Therapy in Classic Infantile Pompe Disease?

血浆或白细胞中的α-葡萄糖苷酶活性能否作为经典婴儿型庞贝病未来基因治疗的生物标志物?

Faraguna, Martha C; Lambregts, Daniël A M; Barzel, Ina; Jacobs, Ed H; Hoogeveen-Westerveld, Marianne; van der Beek, Nadine A M E; Pijnappel, W W M Pim; Gasperini, Serena; Preijers, Tim; van den Hout, Johanna M P; van der Ploeg, Ans T

Correction: Can Alpha-Glucosidase Activity in Plasma or Leukocytes Serve as a Biomarker for Future Gene Therapy in Classic Infantile Pompe Disease?

更正:血浆或白细胞中的α-葡萄糖苷酶活性能否作为经典婴儿型庞贝病未来基因治疗的生物标志物?

Faraguna, Martha C; Lambregts, Daniël A M; Barzel, Ina; Jacobs, Ed H; Hoogeveen-Westerveld, Marianne; van der Beek, Nadine A M E; Pijnappel, W W M Pim; Gasperini, Serena; Preijers, Tim; van den Hout, Johanna M P; van der Ploeg, Ans T

Systemic inflammation impairs myelopoiesis and interferon type I responses in humans

全身性炎症会损害人类的髓系造血和I型干扰素反应。

Farid Keramati # ,Guus P Leijte #,Niklas Bruse #,Inge Grondman,Ehsan Habibi ,Cristian Ruiz-Moreno,Wout Megchelenbrink,Annemieke M Peters van Ton,Hidde Heesakkers,Manita E Bremmers,Erinke van Grinsven,Kiki Tesselaar,Selma van Staveren,Walter J van der Velden,Frank W Preijers,Brigit Te Pas,Raoul van de Loop,Jelle Gerretsen,Mihai G Netea,Hendrik G Stunnenberg,Peter Pickkers,Matthijs Kox

Systemic inflammation impairs myelopoiesis and interferon type I responses in humans

全身性炎症会损害人类的髓系造血和I型干扰素反应。

Keramati, Farid; Leijte, Guus P; Bruse, Niklas; Grondman, Inge; Habibi, Ehsan; Ruiz-Moreno, Cristian; Megchelenbrink, Wout; Peters van Ton, Annemieke M; Heesakkers, Hidde; Bremmers, Manita E; van Grinsven, Erinke; Tesselaar, Kiki; van Staveren, Selma; van der Velden, Walter J; Preijers, Frank W; Te Pas, Brigit; van de Loop, Raoul; Gerretsen, Jelle; Netea, Mihai G; Stunnenberg, Hendrik G; Pickkers, Peter; Kox, Matthijs

Leveraging Clinical Data to Enhance the Performance Evaluation of Ceftriaxone Population Pharmacokinetic Models in Children

利用临床数据提高头孢曲松钠群体药代动力学模型在儿童中的性能评估

Schouwenburg, Stef; Preijers, Tim; Abdulla, Alan; Wildschut, Enno D; Koch, Birgit C P; de Hoog, Matthijs

Effect of Eculizumab on Iron Metabolism in Transfusion-independent Patients With Paroxysmal Nocturnal Hemoglobinuria

依库珠单抗对非输血依赖型阵发性睡眠性血红蛋白尿患者铁代谢的影响

Schaap, Charlotte C M; Schols, Saskia E M; Preijers, Frank W M B; de Jonge, Emiel; Laarakkers, Coby M M; Jansen, Joop H; Blijlevens, Nicole M A; Swinkels, Dorine W; Langemeijer, Saskia M C

Oral and Intravenous Amoxicillin Dosing Recommendations in Neonates: A Pooled Population Pharmacokinetic Study

新生儿口服和静脉注射阿莫西林剂量建议:一项汇总人群药代动力学研究

Keij, Fleur M; Schouwenburg, Stef; Kornelisse, René F; Preijers, Tim; Mir, Fatima; Degraeuwe, Pieter; Stolk, Leo M; van Driel, Arianne; Kenter, Sandra; van der Sluijs, Jacqueline; Heidema, Jojanneke; den Butter, Paul C P; Reiss, Irwin K M; Allegaert, Karel; Tramper-Stranders, Gerdien A; Koch, Birgit C P; Flint, Robert B

The Value of IgM Memory B-Cells in the Assessment of Splenic Function in Childhood Cancer Survivors at Risk for Splenic Dysfunction: A DCCSS-LATER Study

IgM记忆B细胞在评估有脾功能障碍风险的儿童癌症幸存者脾功能中的价值:一项DCCSS-LATER研究

Houtman, Bente M; Walraven, Iris; de Grouw, Elke; van der Maazen, Richard W M; Kremer, Leontien C M; van Dulmen-den Broeder, Eline; van den Heuvel-Eibrink, Marry M; Tissing, Wim J E; Bresters, Dorine; van der Pal, Helena J H; de Vries, Andrica C H; Louwerens, Marloes; van der Heiden-van der Loo, Margriet; Neggers, Sebastian J C; Janssens, Geert O; Blijlevens, Nicole M A; Lambeck, Annechien J A; Preijers, Frank; Loonen, Jacqueline J

Improving the tolerability of osimertinib by identifying its toxic limit

通过确定奥希替尼的毒性极限来提高其耐受性。

Agema, Bram C; Veerman, G D Marijn; Steendam, Christi M J; Lanser, Daan A C; Preijers, Tim; van der Leest, Cor; Koch, Birgit C P; Dingemans, Anne-Marie C; Mathijssen, Ron H J; Koolen, Stijn L W

In silico evaluation of limited sampling strategies for individualized dosing of extended half-life factor IX concentrates in hemophilia B patients

利用计算机模拟评估有限采样策略在B型血友病患者个体化使用长效半衰期因子IX浓缩物中的应用

Preijers, T; van Spengler, M W F; Meijer, K; Fijnvandraat, K; Fischer, K; Leebeek, F W G; Cnossen, M H; Mathôt, R A A