From bench to bedside: preclinical evaluation of a self-inactivating gammaretroviral vector for the gene therapy of X-linked chronic granulomatous disease
从实验室到临床:用于治疗X连锁慢性肉芽肿病的自灭活γ逆转录病毒载体的临床前评估
期刊:Human Gene Therapy Clinical Development
影响因子:
doi:10.1089/humc.2013.019
Stein, Stefan; Scholz, Simone; Schwäble, Joachim; Sadat, Mohammed A; Modlich, Ute; Schultze-Strasser, Stephan; Diaz, Margarita; Chen-Wichmann, Linping; Müller-Kuller, Uta; Brendel, Christian; Fronza, Raffaele; Kaufmann, Kerstin B; Naundorf, Sonja; Pech, Nancy K; Travers, Jeffrey B; Matute, Juan D; Presson, Robert G Jr; Sandusky, George E; Kunkel, Hana; Rudolf, Eva; Dillmann, Adelina; von Kalle, Christof; Kühlcke, Klaus; Baum, Christopher; Schambach, Axel; Dinauer, Mary C; Schmidt, Manfred; Grez, Manuel