日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Consensus-Based Expert Recommendations for Diagnosis and Clinical Management of Vanishing White Matter

基于共识的专家建议:白质消失的诊断和临床管理

van Voorst, Romy J; Schoenmakers, Daphne H; Bonkowsky, Joshua L; Vanderver, Adeline; Krägeloh-Mann, Ingeborg; Bernard, Geneviève; Bertini, Enrico; Fatemi, Ali; Sgobbi, Paulo V; Wolf, Nicole I; Groeschel, Samuel; Tonduti, Davide; Sevin, Caroline; Orthmann-Murphy, Jennifer L; Schöls, Ludger; Salsano, Ettore; Brais, Bernard; Jaffe, Nicole; Ter Horst, Kasper W; Hannema, Sabine E; Hayes, Katherine G; Meyburg, Jochen; van Heerde, Marc; Sbrocchi, Anne Marie; van Spaendonk, Rosalina; Thiffault, Isabelle; Hofsteenge, Geesje H; Sudmeier-Broek, Carolina; Timmer, Corrie; Skwirut, Donna; Buck, Allyson; Hollberg, Bret; Chapleau, Ron; Dekker, Hanka; Campbell, Susan G; Abbink, Truus E M; Leferink, Prisca S; van der Knaap, Marjo S

A simple, field-applicable method to increase the infectivity of wild isolates of Plasmodium falciparum to mosquito vectors

一种简便易行、适用于田间作业的方法,可提高恶性疟原虫野生分离株对蚊媒的感染力。

Ouattara, Seydou Bienvenu; Hien, Domonbabele F D S; Nao, Ekôbié T; Paré, Prisca S L; Guissou, Edwige; Cohuet, Anna; Morlais, Isabelle; Yerbanga, Rakiswendé S; Dabiré, Kounbobr R; Ouédraogo, Jean Bosco; Mouline, Karine; Lefèvre, Thierry

Efficient Purification of Cowpea Chlorotic Mottle Virus by a Novel Peptide Aptamer

新型肽适体高效纯化豇豆褪绿斑驳病毒

Georg Tscheuschner, Marco Ponader, Christopher Raab, Prisca S Weider, Reni Hartfiel, Jan Ole Kaufmann, Jule L Völzke, Gaby Bosc-Bierne, Carsten Prinz, Timm Schwaar, Paul Andrle, Henriette Bäßler, Khoa Nguyen, Yanchen Zhu, Antonia S J S Mey, Amr Mostafa, Ilko Bald, Michael G Weller

Core protocol development for phase 2/3 clinical trials in the leukodystrophy vanishing white matter: a consensus statement by the VWM consortium and patient advocates

脑白质营养不良症(消失性白质)2/3期临床试验核心方案制定:VWM联盟和患者权益倡导者的共识声明

Schoenmakers, Daphne H; Leferink, Prisca S; Vanderver, Adeline; Bonkowsky, Joshua L; Krägeloh-Mann, Ingeborg; Bernard, Geneviève; Bertini, Enrico; Fatemi, Ali; Fogel, Brent L; Wolf, Nicole I; Skwirut, Donna; Buck, Allyson; Holberg, Brett; Saunier-Vivar, Elise F; Rauner, Robert; Dekker, Hanka; van Bokhoven, Pieter; Stellingwerff, Menno D; Berkhof, Johannes; van der Knaap, Marjo S

Therapeutic potential of human stem cell transplantations for Vanishing White Matter: A quest for the Goldilocks graft

人类干细胞移植治疗消失性白质病变的潜力:寻找最佳移植方案

Hillen, Anne E J; Leferink, Prisca S; Breeuwsma, Nicole B; Dooves, Stephanie; Bergaglio, Talia; Van der Knaap, Marjo S; Heine, Vivi M

Therapy Trial Design in Vanishing White Matter: An Expert Consortium Opinion

消失性白质的治疗试验设计:专家联盟意见

van der Knaap, Marjo S; Bonkowsky, Joshua L; Vanderver, Adeline; Schiffmann, Raphael; Krägeloh-Mann, Ingeborg; Bertini, Enrico; Bernard, Genevieve; Fatemi, Seyed Ali; Wolf, Nicole I; Saunier-Vivar, Elise; Rauner, Robert; Dekker, Hanka; van Bokhoven, Pieter; van de Ven, Peter; Leferink, Prisca S

20(th) IUPAB International Congress, 45(th) SBBf Congress and 50(th) Annual Meeting of SBBq: Speaker’s Abstracts

第20届IUPAB国际大会、第45届SBBf大会和第50届SBBq年会:演讲者摘要

van Bokhoven, Pieter; de Wilde, Arno; Vermunt, Lisa; Leferink, Prisca S; Heetveld, Sasja; Cummings, Jeffrey; Scheltens, Philip; Vijverberg, Everard G B

Contrasting effects of the alkaloid ricinine on the capacity of Anopheles gambiae and Anopheles coluzzii to transmit Plasmodium falciparum

蓖麻碱对冈比亚按蚊和古鲁按蚊传播恶性疟原虫能力的对比影响

Domonbabele F D S Hien, Prisca S L Paré, Amanda Cooper, Benjamin K Koama, Edwige Guissou, Koudraogo B Yaméogo, Rakiswendé S Yerbanga, Iain W Farrell, Jean B Ouédraogo, Olivier Gnankiné, Rickard Ignell, Anna Cohuet, Roch K Dabiré, Philip C Stevenson, Thierry Lefèvre

Astrocyte Subtype Vulnerability in Stem Cell Models of Vanishing White Matter

白质消失的干细胞模型中的星形胶质细胞亚型脆弱性

Prisca S Leferink, Stephanie Dooves, Anne E J Hillen, Kyoko Watanabe, Gerbren Jacobs, Lisa Gasparotto, Paulien Cornelissen-Steijger, Marjo S van der Knaap, Vivi M Heine

Astrocyte Subtype Vulnerability in Stem Cell Models of Vanishing White Matter

白质消失干细胞模型中星形胶质细胞亚型的脆弱性

Prisca S Leferink,Stephanie Dooves,Anne E J Hillen,Kyoko Watanabe,Gerbren Jacobs,Lisa Gasparotto,Paulien Cornelissen-Steijger,Marjo S van der Knaap,Vivi M Heine