Intracisternal cyclodextrin prevents cerebellar dysfunction and Purkinje cell death in feline Niemann-Pick type C1 disease
脑池内环糊精可预防猫尼曼-匹克 C1 型病的小脑功能障碍和浦肯野细胞死亡
期刊:Science Translational Medicine
影响因子:15.8
doi:10.1126/scitranslmed.3010101
Charles H Vite, Jessica H Bagel, Gary P Swain, Maria Prociuk, Tracey U Sikora, Veronika M Stein, Patricia O'Donnell, Therese Ruane, Sarah Ward, Alexandra Crooks, Su Li, Elizabeth Mauldin, Susan Stellar, Marc De Meulder, Mark L Kao, Daniel S Ory, Cristin Davidson, Marie T Vanier, Steven U Walkley