日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Outcomes following matched sibling donor transplantation for severe combined immunodeficiency: a report from the PIDTC

同胞相合供体移植治疗重症联合免疫缺陷的疗效:来自PIDTC的报告

Rayes, Ahmad; Logan, Brent R; Liu, Xuerong; Dara, Jasmeen; Buckley, Rebecca H; Oved, Joseph H; Kapoor, Neena; Kapadia, Malika; Chandra, Sharat; Martinez, Caridad A; Bunin, Nancy J; Chandrakasan, Shanmuganathan; Chen, Karin; Bednarski, Jeffrey J; Haines, Hilary L; Eissa, Hesham; Talano, Julie-An M; Keller, Michael D; Ebens, Christen L; Chaudhury, Sonali; Shereck, Evan B; Aquino, Victor M; Knutsen, Alan P; Alexander, Jessie L; Gillio, Alfred P; Chellapandian, Deepakbabu; Shah, Ami J; Miller, Holly K; Vander Lugt, Mark T; Seroogy, Christine M; Dorsey, Morna J; Mousallem, Talal; Parrott, Roberta E; O'Reilly, Richard J; Aguayo-Hiraldo, Paibel I; Prockop, Susan E; Dávila Saldaña, Blachy J; Thakar, Monica S; Burroughs, Lauri M; Torgerson, Troy R; Leiding, Jennifer W; Marsh, Rebecca A; Griffith, Linda M; Pulsipher, Michael A; Kohn, Donald B; Notarangelo, Luigi; Cowan, Morton J; Puck, Jennifer M; Cuvelier, Geoffrey D E; Heimall, Jennifer; Haddad, Elie; Pai, Sung-Yun; Dvorak, Christopher C

Hematopoietic cell transplantation for Wiskott-Aldrich syndrome: a PIDTC report

造血干细胞移植治疗威斯科特-奥尔德里奇综合征:PIDTC报告

Alexander, Jessie L; Dávila Saldaña, Blachy J; Brazauskas, Ruta; Dammalapati, Sravya Gethika; Griffith, Linda M; Shah, Ami J; Shimano, Kristin A; Ochs, Hans D; Bleesing, Jack J; Ebens, Christen L; Kapadia, Malika; Bauchat, Andrea; Kapoor, Neena; Oved, Joseph H; Eissa, Hesham; Lust, Hannah; Keller, Michael D; Haines, Hilary; Chandrakasan, Shanmuganathan; Talano, Julie-An; Rayes, Ahmad; Madden, Lisa; Shereck, Evan; Miller, Holly K; Satter, Lisa Forbes; Martinez, Caridad; Rozmus, Jacob; Bednarski, Jeffrey J; Yu, Lolie C; Chellapandian, Deepakbabu; Aquino, Victor M; Knutsen, Alan; Chong, Hey; Chopek, Ashley; Gillio, Alfred P; Joshi, Avni; Rangarajan, Hemalatha; Moore, Theodore B; Andolina, Jeffrey R; DeSantes, Kenneth B; Vander Lugt, Mark; Prockop, Susan E; Shyr, David C; Sullivan, Kathleen E; Parikh, Suhag; Weinacht, Katja G; Torgerson, Troy R; Marsh, Rebecca; Dvorak, Christopher C; Chan, Alice Y; Haddad, Elie; Heimall, Jennifer R; Pulsipher, Michael A; Leiding, Jennifer W; Kohn, Donald B; Puck, Jennifer M; Notarangelo, Luigi D; Rawlings, David J; Cowan, Morton J; Petrovic, Aleksandra; Pai, Sung-Yun; Burroughs, Lauri M

Acquired Immunodeficiency in Newborn Following Intrauterine Exposure to Thiopurines for Treatment of Inflammatory Bowel Disease

新生儿因宫内暴露于硫嘌呤类药物(用于治疗炎症性肠病)而获得性免疫缺陷

Morand, Susan; Lam, Michael T; Amornsawadwattana, Surachai; Gutierrez, Alexandra; Nguyen, Alan A; Prockop, Susan; Ruggiero, Julie; Kitcharoensakkul, Maleewan

International clinical consensus on leukocyte adhesion deficiency-I: Modified Delphi analysis

关于白细胞黏附缺陷的国际临床共识-I:改良德尔菲分析

Heimall, Jennifer; González-Granado, Luis Ignacio; Booth, Claire; Ip, Winnie; Kuo, Caroline Y; Bakhtiar, Shahrzad; Ikincioğullari, Aydan; Ferrua, Francesca; Chitty-Lopez, Maria; Bailey, Miranda; Carter, Patrice; Matthews, Emily; Lee, Jennifer; Prockop, Susan; Gennery, Andrew R; Leiding, Jennifer W

CAR T cell therapy for children with rheumatic disease: the time is now

CAR-T细胞疗法治疗儿童风湿病:时机已到

Wobma, Holly; Ardoin, Stacy P; Bonifant, Challice L; Cooper, Jennifer C; Kim, Hanna; Sadun, Rebecca E; Lewandowski, Laura; Keller, Michael; Colbert, Robert A; Edens, Cuoghi; DeQuattro, Kimberly; Driest, Kyla; Shalen, Julia; Stojkic, Ivana; Knight, Andrea; Annesley, Colleen; Torok, Kathryn S; Elgarten, Caitlin W; Onishi, Toshihiro; Jackson, Shaun W; Prockop, Susan; Shah, Nirali N; Ardalan, Kaveh; Lamb, Margaret

A single dose of a CD137 antibody-drug conjugate protects rhesus macaque allogeneic HCT recipients against acute GVHD

单剂量CD137抗体药物偶联物可保护恒河猴同种异体造血干细胞移植受者免受急性移植物抗宿主病(GVHD)的侵害。

Gerdemann, Ulrike; Kimler, Kyle; Warren, Matthew R; McGuckin, Connor; Fleming, Ryan A; D'Ambra, Matthew R; Eran, Alal; Albanese, Alexandre; Chen, Edward; Winschel, Marlana; Cagnin, Lorenzo; Lane, Jennifer; Gorfinkel, Lev; Adams, Bartley; Kwun, Jean; Lanieri, Leanne; Hoban, Megan; Lamothe, Tahirih L; Hyzy, Sharon; Olson, Lisa M; Panoskaltsis-Mortari, Angela; Prockop, Susan E; Blazar, Bruce R; Kean, Leslie S; Tkachev, Victor

Allogeneic haematopoietic stem-cell transplantation for children with refractory systemic juvenile idiopathic arthritis and associated lung disease: outcomes from an international, retrospective cohort study

异基因造血干细胞移植治疗难治性全身型幼年特发性关节炎合并肺部疾病患儿:一项国际回顾性队列研究的结果

Matt, Michael G; Drozdov, Daniel; Bendstrup, Elisabeth; Glerup, Mia; Hauge, Ellen-Margrethe; Masmas, Tania; Schneider, Elvira Cannizzaro; Zeilhofer, Ulrike B; Abu-Arja, Rolla F; Driest, Kyla D; Oved, Joseph H; Onel, Karen; Ebens, Christen L; Chellapandian, Deepakbabu; Chandrakasan, Shanmuganathan; Prahalad, Sampath; Roth, Johannes; Prockop, Susan E; Silva, Juliana; Schapiro, Andrew H; Towe, Christopher; Chandra, Sharat; Grom, Alexei; Schulert, Grant S; Marsh, Rebecca A

Multiomics dissection of human RAG deficiency reveals distinctive patterns of immune dysregulation but a common inflammatory signature.

对人类 RAG 缺陷的多组学分析揭示了独特的免疫失调模式,但具有共同的炎症特征。

Bosticardo Marita, Dobbs Kerry, Delmonte Ottavia M, Martins Andrew J, Pala Francesca, Kawai Tomoki, Kenney Heather, Magro Gloria, Rosen Lindsey B, Yamazaki Yasuhiro, Yu Hsin-Hui, Calzoni Enrica, Lee Yu Nee, Liu Can, Stoddard Jennifer, Niemela Julie, Fink Danielle, Castagnoli Riccardo, Ramba Meredith, Cheng Aristine, Riley Deanna, Oikonomou Vasileios, Shaw Elana, Belaid Brahim, Keles Sevgi, Al-Herz Waleed, Cancrini Caterina, Cifaldi Cristina, Baris Safa, Sharapova Svetlana, Schuetz Catharina, Gennery Andrew R, Freeman Alexandra F, Somech Raz, Choo Sharon, Giliani Silvia C, Güngör Tayfun, Drozdov Daniel, Meyts Isabelle, Moshous Despina, Neven Benedicte, Abraham Roshini S, El-Marsafy Aisha, Kanariou Maria, King Alejandra, Licciardi Francesco, Cruz-Muñoz Mario E, Palma Paolo, Poli Cecilia, Adeli Mehdi, Algeri Mattia, Alroqi Fayhan J, Bastard Paul, Bergerson Jenna R E, Booth Claire, Brett Ana, Burns Siobhan O, Butte Manish J, Padem Nurcicek, de la Morena M, Dbaibo Ghassan, de Ravin Suk See, Dimitrova Dimana, Djidjik Reda, Dorna Mayra B, Dutmer Cullen M, Elfeky Reem, Facchetti Fabio, Fuleihan Ramsay L, Geha Raif S, Gonzalez-Granado Luis I, Haljasmägi Liis, Ale Hanadys, Hayward Anthony, Hifanova Anna M, Ip Winnie, Kaplan Blanka, Kapoor Neena, Karakoc-Aydiner Elif, Kärner Jaanika, Keller Michael D, Dávila Saldaña Blachy J, Kiykim Ayça, Kuijpers Taco W, Kuznetsova Elena E, Latysheva Elena A, Leiding Jennifer W, Locatelli Franco, Alva-Lozada Guisela, McCusker Christine, Celmeli Fatih, Morsheimer Megan, Ozen Ahmet, Parvaneh Nima, Pasic Srdjan, Plebani Alessandro, Preece Kahn, Prockop Susan, Sakovich Inga S, Starkova Elena E, Torgerson Troy, Verbsky James, Walter Jolan E, Ward Brant, Wisner Elizabeth L, Draper Deborah, Myint-Hpu Katherine, Truong Pooi M, Lionakis Michail S, Similuk Morgan B, Walkiewicz Magdalena A, Klion Amy, Holland Steven M, Oguz Cihan, Bogunovic Dusan, Kisand Kai, Su Helen C, Tsang John S, Kuhns Douglas, Villa Anna, Rosenzweig Sergio D, Pittaluga Stefania, Notarangelo Luigi D

The Golgi complex governs natural killer cell lytic granule positioning to promote directionality in cytotoxicity

高尔基复合体控制自然杀伤细胞溶解颗粒的定位,从而促进细胞毒性的方向性。

Luis A Pedroza ,Frederique van den Haak ,Alexander Frumovitz ,Evelyn Hernandez ,Everardo Hegewisch-Solloa ,Tabitha K Orange ,Keri B Sheehan ,Susan Prockop ,Aaron Bodansky ,Ivan K Chinn ,James R Lupski ,Jennifer E Posey ,Emily M Mace ,Yu Li ,Jordan S Orange

Allogeneic off-the-shelf CAR T-cell therapy for relapsed or refractory B-cell malignancies

用于治疗复发或难治性B细胞恶性肿瘤的同种异体现成CAR-T细胞疗法

Shahid, Sanam; Prockop, Susan E; Flynn, Georgia C; Mauguen, Audrey; White, Charlie O; Bieler, Jennifer; McAvoy, Devin; Hosszu, Kinga; Cancio, Maria I; Jakubowski, Ann A; Scaradavou, Andromachi; Boelens, Jaap Jan; Sauter, Craig S; Perales, Miguel-Angel; Giralt, Sergio A; Taylor, Clare; Chaudhari, Jagrutiben; Wang, Xiuyan; Rivière, Isabelle; Sadelain, Michel; Brentjens, Renier J; Kernan, Nancy A; O'Reilly, Richard J; Curran, Kevin J