日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Outcomes following matched sibling donor transplantation for severe combined immunodeficiency: a report from the PIDTC

同胞相合供体移植治疗重症联合免疫缺陷的疗效:来自PIDTC的报告

Rayes, Ahmad; Logan, Brent R; Liu, Xuerong; Dara, Jasmeen; Buckley, Rebecca H; Oved, Joseph H; Kapoor, Neena; Kapadia, Malika; Chandra, Sharat; Martinez, Caridad A; Bunin, Nancy J; Chandrakasan, Shanmuganathan; Chen, Karin; Bednarski, Jeffrey J; Haines, Hilary L; Eissa, Hesham; Talano, Julie-An M; Keller, Michael D; Ebens, Christen L; Chaudhury, Sonali; Shereck, Evan B; Aquino, Victor M; Knutsen, Alan P; Alexander, Jessie L; Gillio, Alfred P; Chellapandian, Deepakbabu; Shah, Ami J; Miller, Holly K; Vander Lugt, Mark T; Seroogy, Christine M; Dorsey, Morna J; Mousallem, Talal; Parrott, Roberta E; O'Reilly, Richard J; Aguayo-Hiraldo, Paibel I; Prockop, Susan E; Dávila Saldaña, Blachy J; Thakar, Monica S; Burroughs, Lauri M; Torgerson, Troy R; Leiding, Jennifer W; Marsh, Rebecca A; Griffith, Linda M; Pulsipher, Michael A; Kohn, Donald B; Notarangelo, Luigi; Cowan, Morton J; Puck, Jennifer M; Cuvelier, Geoffrey D E; Heimall, Jennifer; Haddad, Elie; Pai, Sung-Yun; Dvorak, Christopher C

Hematopoietic cell transplantation for Wiskott-Aldrich syndrome: a PIDTC report

造血干细胞移植治疗威斯科特-奥尔德里奇综合征:PIDTC报告

Alexander, Jessie L; Dávila Saldaña, Blachy J; Brazauskas, Ruta; Dammalapati, Sravya Gethika; Griffith, Linda M; Shah, Ami J; Shimano, Kristin A; Ochs, Hans D; Bleesing, Jack J; Ebens, Christen L; Kapadia, Malika; Bauchat, Andrea; Kapoor, Neena; Oved, Joseph H; Eissa, Hesham; Lust, Hannah; Keller, Michael D; Haines, Hilary; Chandrakasan, Shanmuganathan; Talano, Julie-An; Rayes, Ahmad; Madden, Lisa; Shereck, Evan; Miller, Holly K; Satter, Lisa Forbes; Martinez, Caridad; Rozmus, Jacob; Bednarski, Jeffrey J; Yu, Lolie C; Chellapandian, Deepakbabu; Aquino, Victor M; Knutsen, Alan; Chong, Hey; Chopek, Ashley; Gillio, Alfred P; Joshi, Avni; Rangarajan, Hemalatha; Moore, Theodore B; Andolina, Jeffrey R; DeSantes, Kenneth B; Vander Lugt, Mark; Prockop, Susan E; Shyr, David C; Sullivan, Kathleen E; Parikh, Suhag; Weinacht, Katja G; Torgerson, Troy R; Marsh, Rebecca; Dvorak, Christopher C; Chan, Alice Y; Haddad, Elie; Heimall, Jennifer R; Pulsipher, Michael A; Leiding, Jennifer W; Kohn, Donald B; Puck, Jennifer M; Notarangelo, Luigi D; Rawlings, David J; Cowan, Morton J; Petrovic, Aleksandra; Pai, Sung-Yun; Burroughs, Lauri M

A single dose of a CD137 antibody-drug conjugate protects rhesus macaque allogeneic HCT recipients against acute GVHD

单剂量CD137抗体药物偶联物可保护恒河猴同种异体造血干细胞移植受者免受急性移植物抗宿主病(GVHD)的侵害。

Gerdemann, Ulrike; Kimler, Kyle; Warren, Matthew R; McGuckin, Connor; Fleming, Ryan A; D'Ambra, Matthew R; Eran, Alal; Albanese, Alexandre; Chen, Edward; Winschel, Marlana; Cagnin, Lorenzo; Lane, Jennifer; Gorfinkel, Lev; Adams, Bartley; Kwun, Jean; Lanieri, Leanne; Hoban, Megan; Lamothe, Tahirih L; Hyzy, Sharon; Olson, Lisa M; Panoskaltsis-Mortari, Angela; Prockop, Susan E; Blazar, Bruce R; Kean, Leslie S; Tkachev, Victor

Allogeneic haematopoietic stem-cell transplantation for children with refractory systemic juvenile idiopathic arthritis and associated lung disease: outcomes from an international, retrospective cohort study

异基因造血干细胞移植治疗难治性全身型幼年特发性关节炎合并肺部疾病患儿:一项国际回顾性队列研究的结果

Matt, Michael G; Drozdov, Daniel; Bendstrup, Elisabeth; Glerup, Mia; Hauge, Ellen-Margrethe; Masmas, Tania; Schneider, Elvira Cannizzaro; Zeilhofer, Ulrike B; Abu-Arja, Rolla F; Driest, Kyla D; Oved, Joseph H; Onel, Karen; Ebens, Christen L; Chellapandian, Deepakbabu; Chandrakasan, Shanmuganathan; Prahalad, Sampath; Roth, Johannes; Prockop, Susan E; Silva, Juliana; Schapiro, Andrew H; Towe, Christopher; Chandra, Sharat; Grom, Alexei; Schulert, Grant S; Marsh, Rebecca A

Allogeneic off-the-shelf CAR T-cell therapy for relapsed or refractory B-cell malignancies

用于治疗复发或难治性B细胞恶性肿瘤的同种异体现成CAR-T细胞疗法

Shahid, Sanam; Prockop, Susan E; Flynn, Georgia C; Mauguen, Audrey; White, Charlie O; Bieler, Jennifer; McAvoy, Devin; Hosszu, Kinga; Cancio, Maria I; Jakubowski, Ann A; Scaradavou, Andromachi; Boelens, Jaap Jan; Sauter, Craig S; Perales, Miguel-Angel; Giralt, Sergio A; Taylor, Clare; Chaudhari, Jagrutiben; Wang, Xiuyan; Rivière, Isabelle; Sadelain, Michel; Brentjens, Renier J; Kernan, Nancy A; O'Reilly, Richard J; Curran, Kevin J

Harmonized immune recovery monitoring after HCT: evidence and practical guidance from the Westhafen Intercontinental Group

造血干细胞移植后免疫恢复监测的协调统一:来自韦斯特哈芬洲际集团的证据和实践指南

Hammoudi, Taymour; Nucera, Silvia; Troullioud Lucas, Alexandre G; Ansari, Marc; Balduzzi, Adriana; Bertaina, Alice; Buechner, Jochen; Corbacioglu, Selim; Dalle, Jean-Hugues; Kalwak, Krzystof; Lee, Dean; Levine, John E; Lindemans, Caroline A; Locatelli, Franco; Meisel, Roland; Nierkens, Stefan; Ottaviano, Giorgio; Perez-Martinez, Antonio; Pichler, Herbert; Prockop, Susan E; Pulsipher, Michael A; Talano, Julie-An M; Tewari, Sanjay; Schultz, Kirk R; Shah, Nirali N; Verneris, Michael R; Boelens, Jaap Jan

Treating and triggering hyperinflammation: tackling hemophagocytic lymphohistiocytosis and HLH-like syndromes in the pediatric cell therapy and critical care setting

治疗和诱发过度炎症:在儿科细胞治疗和重症监护环境中应对噬血细胞性淋巴组织细胞增生症和HLH样综合征

Wobma, Holly; Henderson, Lauren A; Duncan, Christine N; Prockop, Susan E; Randolph, Adrienne G; Degar, Barbara A; Lehmann, Leslie E; Baumeister, Susanne H C

The role of the conditioning regimen for autologous and ex vivo genetically modified hematopoietic stem cell-based therapies: recommendations from the ISCT stem cell engineering committee

自体和体外基因修饰造血干细胞疗法中预处理方案的作用:ISCT干细胞工程委员会的建议

Oved, Joseph H; Russell, Athena; DeZern, Amy; Prockop, Susan E; Bonfim, Carmem; Sharma, Akshay; Purtill, Duncan; Lakkaraja, Madhavi; Bidgoli, Alan; Bhoopalan, Senthil Velan; Soni, Sandeep; Boelens, Jaap Jan; Abraham, Allistair

Precision Editing of Cyclophilin A Generates Cyclosporine and Voclosporin Resistant Cellular Therapies

对环孢素A进行精准编辑可产生对环孢素和沃克洛孢素耐药的细胞疗法

Wobma, Holly; Alvarez Calderon, Francesca; Dong, Jiayi; Omdahl, Kayleigh; Rui, Xianliang; Rojas Palato, Elisa J; Bermea, Rene S; Albanese, Alexandre; Wachter, Franziska; Winschel, Marlana; Michaelis, Katherine A; Cagnin, Lorenzo; Tkachev, Victor; Prockop, Susan E; Nigrovic, Peter A; Blazar, Bruce R; Gerdemann, Ulrike; Kean, Leslie S

Persistent or New Cytopenias Predict Relapse Better than Routine Bone Marrow Aspirate Evaluations After Hematopoietic Cell Transplantation for Acute Leukemia or Myelodysplastic Syndrome in Children and Young Adult Patients

对于儿童和青少年急性白血病或骨髓增生异常综合征患者,造血干细胞移植后持续性或新发血细胞减少症比常规骨髓穿刺评估更能预测复发。

Kernan, Nancy A; Klein, Elizabeth; Mauguen, Audrey; Torok-Castanza, Joanne; Prockop, Susan E; Scaradavou, Andromachi; Curran, Kevin; Spitzer, Barbara; Cancio, Maria; Ruggiero, Julianne; Allen, Jennifer; Harris, Andrew; Oved, Joseph; O'Reilly, Richard J; Boelens, Jaap Jan