Human cone photoreceptor transplantation stimulates remodeling and restores function in AIPL1 model of end-stage Leber congenital amaurosis
人类视锥细胞光感受器移植可刺激AIPL1终末期Leber先天性黑蒙模型中的重塑并恢复其功能
期刊:Stem Cell Reports
影响因子:5.1
doi:10.1016/j.stemcr.2025.102470
Procyk, Christopher A; Melati, Anna; Ribeiro, Joana; Liu, Jingshu; Branch, Matthew J; Delicata, Jamie D; Tariq, Menahil; Kalarygrou, Aikaterini A; Kapadia, Jessica; Khorsani, Majid Moshtagh; West, Emma L; Smith, Alexander J; Gonzalez-Cordero, Anai; Ali, Robin R; Pearson, Rachael A