日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Biodistribution of AAV1, AAV5, AAV9, and AAVDJ serotypes after intra-cisterna magna delivery in non-human primates

非人灵长类动物经枕大池内给药后AAV1、AAV5、AAV9和AAVDJ血清型的生物分布

Okai, Takuro; Sato, Sho; Yasuno, Hironobu; Nakayama, Miyu; Yamamoto, Syunsuke; Sjöqvist, Sebastian; Otake, Kentaro; Nakashima, Masato; Deshpande, Mugdha; Galbreath, Elizabeth; Oak, Jeong-Ho; Miyamoto, Saku; Proetzel, Gabriele

AAV delivery of GBA1 suppresses α-synuclein accumulation in Parkinson's disease models and restores functions in Gaucher's disease models.

AAV递送GBA1可抑制帕金森病模型中α-突触核蛋白的积累,并恢复戈谢病模型中的功能

Okai Takuro, Sato Sho, Deshpande Mugdha, Matsumoto Shin-Ichi, Nakayama Miyu, Yamamoto Syunsuke, Strack-Logue Bettina, Hioki Takeshi, Tanaka Maiko, Proetzel Gabriele

Hematopoietic cells as site of first-pass catabolism after subcutaneous dosing and contributors to systemic clearance of a monoclonal antibody in mice

小鼠皮下注射单克隆抗体后,造血细胞是首过代谢的部位,并参与单克隆抗体的全身清除。

Richter, Wolfgang F; Christianson, Gregory J; Frances, Nicolas; Grimm, Hans Peter; Proetzel, Gabriele; Roopenian, Derry C

Albumin-deficient mouse models for studying metabolism of human albumin and pharmacokinetics of albumin-based drugs

用于研究人体白蛋白代谢和白蛋白类药物药代动力学的白蛋白缺乏小鼠模型

Derry C Roopenian, Benjamin E Low, Gregory J Christianson, Gabriele Proetzel, Thomas J Sproule, Michael V Wiles

Genetically engineered humanized mouse models for preclinical antibody studies

用于临床前抗体研究的基因工程人源化小鼠模型

Proetzel, Gabriele; Wiles, Michael V; Roopenian, Derry C

Humanized FcRn mouse models for evaluating pharmacokinetics of human IgG antibodies

用于评估人类 IgG 抗体药代动力学的人源化 FcRn 小鼠模型

Gabriele Proetzel, Derry C Roopenian

Monoclonal antibodies directed against human FcRn and their applications

针对人FcRn的单克隆抗体及其应用

Gregory J Christianson, Victor Z Sun, Shreeram Akilesh, Emanuele Pesavento, Gabriele Proetzel, Derry C Roopenian

Transforming growth factor-beta 3 is required for secondary palate fusion

转化生长因子-β3是腭二次融合所必需的

Proetzel, G; Pawlowski, S A; Wiles, M V; Yin, M; Boivin, G P; Howles, P N; Ding, J; Ferguson, M W; Doetschman, T