日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Biodistribution of AAV1, AAV5, AAV9, and AAVDJ serotypes after intra-cisterna magna delivery in non-human primates

非人灵长类动物经枕大池内给药后AAV1、AAV5、AAV9和AAVDJ血清型的生物分布

Okai, Takuro; Sato, Sho; Yasuno, Hironobu; Nakayama, Miyu; Yamamoto, Syunsuke; Sjöqvist, Sebastian; Otake, Kentaro; Nakashima, Masato; Deshpande, Mugdha; Galbreath, Elizabeth; Oak, Jeong-Ho; Miyamoto, Saku; Proetzel, Gabriele

AAV delivery of GBA1 suppresses α-synuclein accumulation in Parkinson's disease models and restores functions in Gaucher's disease models.

AAV递送GBA1可抑制帕金森病模型中α-突触核蛋白的积累,并恢复戈谢病模型中的功能

Okai Takuro, Sato Sho, Deshpande Mugdha, Matsumoto Shin-Ichi, Nakayama Miyu, Yamamoto Syunsuke, Strack-Logue Bettina, Hioki Takeshi, Tanaka Maiko, Proetzel Gabriele

Hematopoietic cells as site of first-pass catabolism after subcutaneous dosing and contributors to systemic clearance of a monoclonal antibody in mice

小鼠皮下注射单克隆抗体后,造血细胞是首过代谢的部位,并参与单克隆抗体的全身清除。

Richter, Wolfgang F; Christianson, Gregory J; Frances, Nicolas; Grimm, Hans Peter; Proetzel, Gabriele; Roopenian, Derry C

Genetically engineered humanized mouse models for preclinical antibody studies

用于临床前抗体研究的基因工程人源化小鼠模型

Proetzel, Gabriele; Wiles, Michael V; Roopenian, Derry C