Biodistribution of AAV1, AAV5, AAV9, and AAVDJ serotypes after intra-cisterna magna delivery in non-human primates
非人灵长类动物经枕大池内给药后AAV1、AAV5、AAV9和AAVDJ血清型的生物分布
期刊:Molecular Therapy-Methods & Clinical Development
影响因子:4.7
doi:10.1016/j.omtm.2025.101593
Okai, Takuro; Sato, Sho; Yasuno, Hironobu; Nakayama, Miyu; Yamamoto, Syunsuke; Sjöqvist, Sebastian; Otake, Kentaro; Nakashima, Masato; Deshpande, Mugdha; Galbreath, Elizabeth; Oak, Jeong-Ho; Miyamoto, Saku; Proetzel, Gabriele