日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Lentivirus-mediated gene therapy for Fabry disease

慢病毒介导的基因疗法治疗法布里病

Khan, Aneal; Barber, Dwayne L; Huang, Ju; Rupar, C Anthony; Rip, Jack W; Auray-Blais, Christiane; Boutin, Michel; O'Hoski, Pamela; Gargulak, Kristy; McKillop, William M; Fraser, Graeme; Wasim, Syed; LeMoine, Kaye; Jelinski, Shelly; Chaudhry, Ahsan; Prokopishyn, Nicole; Morel, Chantal F; Couban, Stephen; Duggan, Peter R; Fowler, Daniel H; Keating, Armand; West, Michael L; Foley, Ronan; Medin, Jeffrey A

The Concentration of Total Nucleated Cells in Harvested Bone Marrow for Transplantation Has Decreased over Time

随着时间的推移,用于移植的骨髓中总有核细胞浓度有所下降。

Prokopishyn, Nicole L; Logan, Brent R; Kiefer, Deidre M; Sees, Jennifer A; Chitphakdithai, Pintip; Ahmed, Ibrahim A; Anderlini, Paolo N; Beitinjaneh, Amer M; Bredeson, Christopher; Cerny, Jan; Chhabra, Saurabh; Daly, Andrew; Diaz, Miguel Angel; Farhadfar, Nosha; Frangoul, Haydar A; Ganguly, Siddhartha; Gastineau, Dennis A; Gergis, Usama; Hale, Gregory A; Hematti, Peiman; Kamble, Rammurti T; Kasow, Kimberly A; Lazarus, Hillard M; Liesveld, Jane L; Murthy, Hemant S; Norkin, Maxim; Olsson, Richard F; Papari, Mona; Savani, Bipin N; Szer, Jeffrey; Waller, Edmund K; Wirk, Baldeep; Yared, Jean A; Pulsipher, Michael A; Shah, Nirali N; Switzer, Galen E; O'Donnell, Paul V; Confer, Dennis L; Shaw, Bronwen E

Lentivector Iterations and Pre-Clinical Scale-Up/Toxicity Testing: Targeting Mobilized CD34+ Cells for Correction of Fabry Disease

慢病毒载体迭代和临床前扩大/毒性测试:针对动员的 CD34+ 细胞治疗法布里病

Ju Huang, Aneal Khan, Bryan C Au, Dwayne L Barber, Lucía López-Vásquez, Nicole L Prokopishyn, Michel Boutin, Michael Rothe, Jack W Rip, Mona Abaoui, Murtaza S Nagree, Shaalee Dworski, Axel Schambach, Armand Keating, Michael L West, John Klassen, Patricia V Turner, Sandra Sirrs, C Anthony Rupar, Chri

Unprecedented diversity of genotypic revertants in lymphocytes of a patient with Wiskott-Aldrich syndrome

威斯科特-奥尔德里奇综合征患者淋巴细胞中基因型回复突变的多样性前所未有

Brian R Davis, Michael J Dicola, Nicole L Prokopishyn, Jonathan B Rosenberg, Daniele Moratto, Linda M Muul, Fabio Candotti, R Michael Blaese