Muscle-specific gene editing improves molecular and phenotypic defects in a mouse model of myotonic dystrophy type 1
肌肉特异性基因编辑改善了1型强直性肌营养不良小鼠模型的分子和表型缺陷
期刊:Clinical and Translational Medicine
影响因子:6.8
doi:10.1002/ctm2.70227
Izzo, Mariapaola; Battistini, Jonathan; Golini, Elisabetta; Voellenkle, Christine; Provenzano, Claudia; Orsini, Tiziana; Strimpakos, Georgios; Scavizzi, Ferdinando; Raspa, Marcello; Baci, Denisa; Frolova, Svetlana; Tastsoglou, Spyros; Zaccagnini, Germana; Garcia-Manteiga, Jose Manuel; Gourdon, Genevieve; Mandillo, Silvia; Cardinali, Beatrice; Martelli, Fabio; Falcone, Germana
