日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Large-scale discovery of potent, compact and erythroid specific enhancers for gene therapy vectors.

大规模发现用于基因治疗载体的高效、紧凑且红系特异性增强子

Psatha Nikoletta, Sova Pavel, Georgolopoulos Grigorios, Paschoudi Kiriaki, Iwata Mineo, Bloom Jordan, Ulyanova Tatyana, Wang Hao, Kirtsou Alexandra, Vasiloudis Ninos-Ioannis, Wilken Matthew S, Stamatoyannopoulos John A, Yannaki Evangelia, Papayanopoulou Thalia, Stamatoyannopoulos George, Vierstra Jeff

Epigenetic Regulation of Erythropoiesis: From Developmental Programs to Therapeutic Targets

红细胞生成的表观遗传调控:从发育程序到治疗靶点

Vasiloudis, Ninos Ioannis; Paschoudi, Kiriaki; Beta, Christina; Georgolopoulos, Grigorios; Psatha, Nikoletta

Precision Editing as a Therapeutic Approach for β-Hemoglobinopathies

精准编辑作为β-血红蛋白病的一种治疗方法

Paschoudi, Kiriaki; Yannaki, Evangelia; Psatha, Nikoletta

In Vivo Hematopoietic Stem Cell Genome Editing: Perspectives and Limitations

体内造血干细胞基因组编辑:前景与局限性

Psatha, Nikoletta; Paschoudi, Kiriaki; Papadopoulou, Anastasia; Yannaki, Evangelia

Enhanced HbF reactivation by multiplex mutagenesis of thalassemic CD34+ cells in vitro and in vivo

体外和体内通过对地中海贫血CD34+细胞进行多重诱变增强HbF再激活

Psatha, Nikoletta; Georgakopoulou, Aphrodite; Li, Chang; Nandakumar, Vivek; Georgolopoulos, Grigorios; Acosta, Reyes; Paschoudi, Kiriaki; Nelson, Jemma; Chee, Daniel; Athanasiadou, Anastasia; Kouvatsi, Anastasia; Funnell, Alister Peter William; Lieber, André; Yannaki, Evangelia; Papayannopoulou, Thalia

Investigating the Barrier Activity of Novel, Human Enhancer-Blocking Chromatin Insulators for Hematopoietic Stem Cell Gene Therapy

研究新型人类增强子阻断染色质绝缘子在造血干细胞基因治疗中的屏障活性

Papayanni, Penelope-Georgia; Psatha, Nikoletta; Christofi, Panayota; Li, Xing-Guo; Melo, Pamela; Volpin, Monica; Montini, Eugenio; Liu, Mingdong; Kaltsounis, Georgios; Yiangou, Minas; Emery, David W; Anagnostopoulos, Achilles; Papayannopoulou, Thalia; Huang, Suming; Stamatoyannopoulos, George; Yannaki, Evangelia

"Cerberus" T Cells: A Glucocorticoid-Resistant, Multi-Pathogen Specific T Cell Product to Fight Infections in Severely Immunocompromised Patients

“刻耳柏洛斯”T细胞:一种耐糖皮质激素、多病原体特异性T细胞产品,用于对抗严重免疫功能低下患者的感染

Koukoulias, Kiriakos; Papayanni, Penelope-Georgia; Georgakopoulou, Aphrodite; Alvanou, Maria; Laidou, Stamatia; Kouimtzidis, Anastasios; Pantazi, Chrysoula; Gkoliou, Glykeria; Vyzantiadis, Timoleon-Achilleas; Spyridonidis, Alexandros; Makris, Antonios; Chatzidimitriou, Anastasia; Psatha, Nikoletta; Anagnostopoulos, Achilles; Yannaki, Evangelia; Papadopoulou, Anastasia

Unbiased phenotypic identification of functionally distinct hematopoietic progenitors

无偏倚的表型鉴定功能不同的造血祖细胞

Georgolopoulos, Grigorios; Iwata, Mineo; Psatha, Nikoletta; Yiangou, Minas; Vierstra, Jeff

Integrating HDAd5/35++ Vectors as a New Platform for HSC Gene Therapy of Hemoglobinopathies

将HDAd5/35++载体整合为造血干细胞基因治疗血红蛋白病的新平台

Li, Chang; Psatha, Nikoletta; Wang, Hongjie; Singh, Manvendra; Samal, Himanshu Bhusan; Zhang, Wenli; Ehrhardt, Anja; Izsvák, Zsuzsanna; Papayannopoulou, Thalia; Lieber, André

A Combined In Vivo HSC Transduction/Selection Approach Results in Efficient and Stable Gene Expression in Peripheral Blood Cells in Mice

体内造血干细胞转导/筛选相结合的方法可实现小鼠外周血细胞中高效稳定的基因表达

Wang, Hongjie; Richter, Maximilian; Psatha, Nikoletta; Li, Chang; Kim, Jiho; Liu, Jing; Ehrhardt, Anja; Nilsson, Susan K; Cao, Benjamin; Palmer, Donna; Ng, Philip; Izsvák, Zsuzsanna; Haworth, Kevin G; Kiem, Hans-Peter; Papayannopoulou, Thalia; Lieber, André