Intravitreal Enzyme Replacement Therapy Slows Retinopathy in Late Infantile Ceroid Lipofuscinosis Type 2
玻璃体内酶替代疗法可延缓晚期婴儿型2型蜡样脂褐质沉积症的视网膜病变进展
期刊:Neuropediatrics
影响因子:1.2
doi:10.1055/a-2510-5592
Priglinger, Claudia S; Courage, Carolina; Lotz-Havla, Amelie S; Gerhardt, Maximilian; Ehrt, Oliver; Kurz, Matthias; Pudritz, Harald; Rudolph, Günther; Jackson, Christopher B; Maier, Esther M