日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Distinct biological subtypes of chronic GVHD after pediatric hematopoietic cell transplantation

儿童造血干细胞移植后慢性移植物抗宿主病的不同生物学亚型

Ng, Bernard; Harris, Andrew C; Abdossamadi, Sayeh; Aubert, Geraldine; Bajwa, Rajinder; Bhatia, Monica; Bittencourt, Henrique; Buxbaum, Nataliya P; Caywood, Emi H; Chaudhury, Sonali; Chewning, Joseph H; Choi, Sung Won; Chopek, Ashley; Chu, Julia; Coulter, Donald; Gadalla, Shahinaz M; Hogg, Richard T; Jacobsohn, David A; Johnson, Amanda K; Joyce, Michael; Kasow, Kimberly A; Kent, Michael; Kitko, Carrie L; Lau, Donna; Lawitschka, Anita; Lewis, Victor A; Li, Amanda M; McLaughlin, Laura; Mitchell, David; Nemecek, Eneida R; Parthasarathy, Vaishnavi; Pawlowska, Anna B; Pirsl, Filip; Pulsipher, Michael A; Qayed, Muna; Rozmus, Jacob; Savaşan, Süreyya; Schechter, Tal; Shenoy, Shalini; Suleimenova, Alima; Zheng, Dong Jun; Ostroumov, Elena; Gilman, Andrew; Klein Geltink, Ramon I; Wolff, Daniel; Cuvelier, Geoffrey D E; Schultz, Kirk R

Outcomes following matched sibling donor transplantation for severe combined immunodeficiency: a report from the PIDTC

同胞相合供体移植治疗重症联合免疫缺陷的疗效:来自PIDTC的报告

Rayes, Ahmad; Logan, Brent R; Liu, Xuerong; Dara, Jasmeen; Buckley, Rebecca H; Oved, Joseph H; Kapoor, Neena; Kapadia, Malika; Chandra, Sharat; Martinez, Caridad A; Bunin, Nancy J; Chandrakasan, Shanmuganathan; Chen, Karin; Bednarski, Jeffrey J; Haines, Hilary L; Eissa, Hesham; Talano, Julie-An M; Keller, Michael D; Ebens, Christen L; Chaudhury, Sonali; Shereck, Evan B; Aquino, Victor M; Knutsen, Alan P; Alexander, Jessie L; Gillio, Alfred P; Chellapandian, Deepakbabu; Shah, Ami J; Miller, Holly K; Vander Lugt, Mark T; Seroogy, Christine M; Dorsey, Morna J; Mousallem, Talal; Parrott, Roberta E; O'Reilly, Richard J; Aguayo-Hiraldo, Paibel I; Prockop, Susan E; Dávila Saldaña, Blachy J; Thakar, Monica S; Burroughs, Lauri M; Torgerson, Troy R; Leiding, Jennifer W; Marsh, Rebecca A; Griffith, Linda M; Pulsipher, Michael A; Kohn, Donald B; Notarangelo, Luigi; Cowan, Morton J; Puck, Jennifer M; Cuvelier, Geoffrey D E; Heimall, Jennifer; Haddad, Elie; Pai, Sung-Yun; Dvorak, Christopher C

Hematopoietic cell transplantation for Wiskott-Aldrich syndrome: a PIDTC report

造血干细胞移植治疗威斯科特-奥尔德里奇综合征:PIDTC报告

Alexander, Jessie L; Dávila Saldaña, Blachy J; Brazauskas, Ruta; Dammalapati, Sravya Gethika; Griffith, Linda M; Shah, Ami J; Shimano, Kristin A; Ochs, Hans D; Bleesing, Jack J; Ebens, Christen L; Kapadia, Malika; Bauchat, Andrea; Kapoor, Neena; Oved, Joseph H; Eissa, Hesham; Lust, Hannah; Keller, Michael D; Haines, Hilary; Chandrakasan, Shanmuganathan; Talano, Julie-An; Rayes, Ahmad; Madden, Lisa; Shereck, Evan; Miller, Holly K; Satter, Lisa Forbes; Martinez, Caridad; Rozmus, Jacob; Bednarski, Jeffrey J; Yu, Lolie C; Chellapandian, Deepakbabu; Aquino, Victor M; Knutsen, Alan; Chong, Hey; Chopek, Ashley; Gillio, Alfred P; Joshi, Avni; Rangarajan, Hemalatha; Moore, Theodore B; Andolina, Jeffrey R; DeSantes, Kenneth B; Vander Lugt, Mark; Prockop, Susan E; Shyr, David C; Sullivan, Kathleen E; Parikh, Suhag; Weinacht, Katja G; Torgerson, Troy R; Marsh, Rebecca; Dvorak, Christopher C; Chan, Alice Y; Haddad, Elie; Heimall, Jennifer R; Pulsipher, Michael A; Leiding, Jennifer W; Kohn, Donald B; Puck, Jennifer M; Notarangelo, Luigi D; Rawlings, David J; Cowan, Morton J; Petrovic, Aleksandra; Pai, Sung-Yun; Burroughs, Lauri M

Umbilical Cord Blood Transplantation Provides an Alternative for Patients With Chronic Granulomatous Disease Lacking HLA-Matched Donors: A PIDTC Report

脐带血移植为缺乏HLA匹配供体的慢性肉芽肿病患者提供了一种替代方案:PIDTC报告

Arnold, Danielle E; Leiding, Jennifer W; Logan, Brent; Marsh, Rebecca A; Griffith, Linda M; Grunebaum, Eyal; Murguía-Favela, Luis; Mallhi, Kanwaldeep; Chellapandian, Deepakbabu; Deal, Christin L; Lim, Stephanie Si; Prasad, Vinod; Heimall, Jennifer; Chandrakasan, Shanmuganathan; Chen, Karin; Yu, Lolie C; Seroogy, Christine M; Gillio, Alfred; Bednarski, Jeffrey J; Kapoor, Neena; Moore, Theodore B; Cuvelier, Geoffrey D E; Touzot, Fabien; Rayes, Ahmad; Ebens, Christen L; Schaefer, Edo; Bauchat, Andrea; Chopek, Ashley; Burroughs, Lauri; Cowan, Morton J; Dvorak, Christopher C; Haddad, Elie; Kohn, Donald B; Notarangelo, Luigi D; Pai, Sung-Yun; Puck, Jennifer M; Pulsipher, Michael A; Torgerson, Troy; Malech, Harry L; Kang, Elizabeth M; Parikh, Suhag

Identification of Distinct Subtypes in Immune Tolerance after Hematopoietic Cell Transplantation Using the Prospective ABLE1.0 Pediatric Study Cohort

利用前瞻性ABLE1.0儿科研究队列鉴定造血细胞移植后免疫耐受的不同亚型

Ng, Bernard; Harris, Andrew C; Abdossamadi, Sayeh; Lauener, Madeline P; Aubert, Geraldine; Bajwa, Rajinder; Bhatia, Monica; Bittencourt, Henrique; Buxbaum, Nataliya P; Caywood, Emi H; Chaudhury, Sonali; Chewning, Joseph H; Choi, Sung Won; Chopek, Ashley; Chu, Julia; Coulter, Donald; Gadalla, Shahinaz M; Hogg, Richard T; Jacobsohn, David A; Johnson, Amanda K; Joyce, Michael; Kasow, Kimberly A; Kent, Michael; Kitko, Carrie L; Lau, Donna; Lawitschka, Anita; Lewis, Victor A; Li, Amanda M; McLaughlin, Laura; Mitchell, David; Nemecek, Eneida R; Parthasarathy, Vaishnavi; Pawlowska, Anna B; Pirsl, Filip; Pulsipher, Michael A; Qayed, Muna; Rozmus, Jacob; Savaşan, Süreyya; Schechter, Tal; Shenoy, Shalini; Suleimenova, Alima; Zheng, Dong Jun; Ostroumov, Elena; Geltink, Ramon I Klein; Gilman, Andrew; Wolff, Daniel; Cuvelier, Geoffrey D E; Schultz, Kirk R

Clinical spectrum of Wiskott-Aldrich syndrome carriers: Self-reported survey of 193 carriers

Wiskott-Aldrich综合征携带者的临床表现谱:193名携带者的自我报告调查

Chandrakasan, Shanmuganathan; Westbrook, Adrianna; Griffith, Linda M; Hagin, David; Iyengar, Sumathi; Mangurian, Christina; Scalchunes, Chris; Sullivan, Kathleen E; Zablocki, Akiva; Bakshi, Nitya; Sinha, Cynthia; Burroughs, Lauri M; Chan, Alice Y; Dvorak, Christopher C; Haddad, Elie; Heimall, Jennifer; Kohn, Donald B; Leiding, Jennifer W; Notarangelo, Luigi D; Pai, Sung-Yun; Puck, Jennifer M; Pulsipher, Michael A; Marsh, Rebecca A; Torgerson, Troy; Cowan, Morton J; Ochs, Hans D; Parikh, Suhag

Neurodevelopmental outcomes following hematopoietic cell transplantation for patients with severe combined immunodeficiency (SCID): A PIDTC study

造血干细胞移植治疗重症联合免疫缺陷(SCID)患者的神经发育结局:一项PIDTC研究

Brumm, Virdette L; Kidd, Sharon A; Logan, Brent R; Chunara, Farheen; Heimall, Jennifer; Griffith, Linda M; Kohn, Donald B; Sanchez, Lauren; Bednarski, Jeffrey J; Martinez, Caridad; Lugt, Mark Vander; Kapoor, Neena; Wright, Nicola; Spitzer, Barbara; Oved, Joseph H; Chandra, Sharat; Chellapandian, Deepak; Ebens, Christen L; Petrovic, Aleks; Rayes, Ahmad; Haines, Hilary L; Lust, Hannah; Schofield, Hannah-Lise Tirado; Christopher, Lauren; Harris, Lynnette L; Satter, Lisa Forbes; Burroughs, Lauri; Dvorak, Christopher C; Haddad, Elie; Leiding, Jennifer W; Marsh, Rebecca A; Notarangelo, Luigi D; Pai, Sung Yun; Pulsipher, Michael A; Puck, Jennifer M; Cowan, Morton J; Shah, Ami J

Refractory infantile IPEX with Treg-restricted FOXP3null expression caused by a novel variant in FOXP3.

由 FOXP3 中的一种新变异引起的 Treg 限制性 FOXP3null 表达的难治性婴儿 IPEX。

Rayes Ahmad, Ramachandran Akshaya, Pulsipher Michael A, Dolan J Gregory, Cho Soohee, Johnson Amanda K, Alexander Jessie L, Borna Simon, Bacchetta Rosa

Outcomes of PLAT-02 and PLAT-03: evaluating CD19 CAR T-cell therapy and CD19-expressing T-APC support in pediatric B-ALL

PLAT-02 和 PLAT-03 研究结果:评估 CD19 CAR T 细胞疗法和表达 CD19 的 T-APC 支持治疗儿童 B 细胞急性淋巴细胞白血病 (B-ALL) 的疗效

Annesley, Colleen; Seidel, Kristy; Wu, Qian; Summers, Corinne; Wayne, Alan S; Pulsipher, Michael A; Agrawal, Anurag K; Brown, Chris T; Mgebroff, Stephanie; Lindgren, Catherine; Rawlings-Rhea, Stephanie; Huang, Wenjun; Wilson, Ashley L; Jensen, Michael C; Park, Julie R; Gardner, Rebecca A

Harmonization on defining B-cell recovery post CD19-CAR T-cell therapy in B-cell acute lymphoblastic leukemia: An international consensus statement

关于CD19-CAR T细胞疗法治疗B细胞急性淋巴细胞白血病后B细胞恢复定义的协调统一:一项国际共识声明

Lamble, Adam; Bohling, Sandra D; Davis, Kara L; Talleur, Aimee C; McNerney, Kevin O; Naik, Swati; Kumar, Priya; Thomas, Rebecca; Wang, Hao-Wei; Yuan, Constance M; Jacoby, Elad; Baruchel, Andre; Ghorashian, Sara; Pulsipher, Michael A; Schultz, Liora; Gardner, Rebecca A; Shah, Nirali N