日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Modification of the VP1u region boosts transduction of adeno-associated virus vectors for ocular gene therapy.

VP1u 区域的修饰可增强腺相关病毒载体在眼部基因治疗中的转导。

Cui Mengtian, Cheng Shun-Yun, Liang Jialing, McGowan Jackson, Xu Meiyu, Xu Guangchao, Luo Li, Wu Joae, Harman Christine D, Jacobson Amanda L, Kapeller Lydia E, Mayes Melaney A, Namkung Suk, Sharma Tapan, Leland Thomas B, Zhang Fang, Yip Mitchell, Rossmiller Brian, Xue Thomas, Chen Xiupeng, Boonying Wassamon, Lotun Anoushka, Wang Dan, Su Qin, Xie Jun, Wei Yuquan, Rothstein Ann M, Gregory-Ksander Meredith S, Komaromy Andras, Tian Bo, Lin Haijiang, Punzo Claudio, Tai Phillip W L, Gao Guangping

An siRNA targeting S6k1 identifies photoreceptor phospholipid metabolism as a contributor to lipid buildup in age-related macular degeneration.

针对 S6k1 的 siRNA 发现光感受器磷脂代谢是导致年龄相关性黄斑变性中脂质积累的因素之一。

Cheng Shun-Yun, Giguere Delaney, Kim San, Seddon Johanna M, Caiazzi Jillian, Gross Katherine, McHugh Nicholas, Echeverria Dimas, Alterman Julia F, Gray-Edwards Heather, Benatti Hector Ribeiro, Renner Lauren, Woolard Hannah, Stoddard Jonathan, McGill Trevor J, Neuringer Martha, Brush Richard S, Agbaga Martin-Paul, Khvorova Anastasia, Punzo Claudio

Update on Gene Therapy Clinical Trials for Eye Diseases

眼科疾病基因治疗临床试验最新进展

Lonfat, Nicolas; Moreno-Leon, Laura; Punzo, Claudio; Khanna, Hemant

Role of alpha-1 antitrypsin in Bruch's membrane integrity.

α1-抗胰蛋白酶在布鲁赫膜完整性中的作用

Cheng Shun-Yun, Giguere Delaney, Silverstein Ilana, Conza Adrienne, Seddon Johanna M, Kim San, Iwata Takeshi, Mueller Christian, Punzo Claudio

Update on Viral Gene Therapy Clinical Trials for Retinal Diseases

视网膜疾病病毒基因疗法临床试验最新进展

Cheng, Shun-Yun; Punzo, Claudio

2015 William Allan Award Introduction: Kay E. Davies

2015年威廉·艾伦奖介绍:凯·E·戴维斯

Petit, Lolita; Khanna, Hemant; Punzo, Claudio; Fisch, Gene S

Quantifying the metabolic contribution to photoreceptor death in retinitis pigmentosa via a mathematical model

利用数学模型量化色素性视网膜炎中代谢因素对感光细胞死亡的贡献

Camacho, Erika T; Punzo, Claudio; Wirkus, Stephen A

mTORC1 sustains vision in retinitis pigmentosa

mTORC1在视网膜色素变性中维持视力

Petit, Lolita; Punzo, Claudio

Replication-dependent histone genes are actively transcribed in differentiating and aging retinal neurons

在分化和衰老的视网膜神经元中,复制依赖性组蛋白基因被积极转录。

Banday, Abdul Rouf; Baumgartner, Marybeth; Al Seesi, Sahar; Karunakaran, Devi Krishna Priya; Venkatesh, Aditya; Congdon, Sean; Lemoine, Christopher; Kilcollins, Ashley M; Mandoiu, Ion; Punzo, Claudio; Kanadia, Rahul N

Retinal gene delivery by rAAV and DNA electroporation

利用rAAV和DNA电穿孔进行视网膜基因递送

Venkatesh, Aditya; Ma, Shan; Langellotto, Fernanda; Gao, Guangping; Punzo, Claudio