Efficacy and muscle safety assessment of fukutin-related protein gene therapy.
福库汀相关蛋白基因疗法的疗效和肌肉安全性评估
期刊:Molecular Therapy-Methods & Clinical Development
影响因子:4.7
doi:10.1016/j.omtm.2023.05.022
Benasutti Halli, Maricelli Joseph W, Seto Jane, Hall John, Halbert Christine, Wicki Jacqueline, Heusgen Lydia, Purvis Nicholas, Regnier Michael, Lin David C, Rodgers Buel D, Chamberlain Jeffrey S