Meaningful Endpoints for Idiopathic Pulmonary Fibrosis (IPF) Clinical Trials: Emphasis on 'Feels, Functions, Survives'. Report of a Collaborative Discussion in a Symposium with Direct Engagement from Representatives of Patients, Investigators, the National Institutes of Health, a Patient Advocacy Organization, and a Regulatory Agency
特发性肺纤维化(IPF)临床试验的有效终点:重点关注“感觉、功能和生存”。这是一份由患者代表、研究人员、美国国立卫生研究院、患者权益组织和监管机构代表共同参与的研讨会合作讨论报告。
期刊:American Journal of Respiratory and Critical Care Medicine
影响因子:19.4
doi:10.1164/rccm.202312-2213SO
Raghu, Ganesh; Ghazipura, Marya; Fleming, Thomas R; Aronson, Kerri I; Behr, Jürgen; Brown, Kevin K; Flaherty, Kevin R; Kazerooni, Ella A; Maher, Toby M; Richeldi, Luca; Lasky, Joseph A; Swigris, Jeffrey J; Busch, Robert; Garrard, Lili; Ahn, Dong-Hyun; Li, Ji; Puthawala, Khalid; Rodal, Gabriela; Seymour, Sally; Weir, Nargues; Danoff, Sonye K; Ettinger, Neil; Goldin, Jonathan; Glassberg, Marilyn K; Kawano-Dourado, Leticia; Khalil, Nasreen; Lancaster, Lisa; Lynch, David A; Mageto, Yolanda; Noth, Imre; Shore, Jessica E; Wijsenbeek, Marlies; Brown, Robert; Grogan, Daniel; Ivey, Dorothy; Golinska, Patrycja; Karimi-Shah, Banu; Martinez, Fernando J