日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Therapeutic strategies for diffuse midline glioma from high-throughput combination drug screening

基于高通量联合药物筛选的弥漫性中线胶质瘤治疗策略

Lin, Grant L; Wilson, Kelli M; Ceribelli, Michele; Stanton, Benjamin Z; Woo, Pamelyn J; Kreimer, Sara; Qin, Elizabeth Y; Zhang, Xiaohu; Lennon, James; Nagaraja, Surya; Morris, Patrick J; Quezada, Michael; Gillespie, Shawn M; Duveau, Damien Y; Michalowski, Aleksandra M; Shinn, Paul; Guha, Rajarshi; Ferrer, Marc; Klumpp-Thomas, Carleen; Michael, Sam; McKnight, Crystal; Minhas, Paras; Itkin, Zina; Raabe, Eric H; Chen, Lu; Ghanem, Reem; Geraghty, Anna C; Ni, Lijun; Andreasson, Katrin I; Vitanza, Nicholas A; Warren, Katherine E; Thomas, Craig J; Monje, Michelle

Mechanism-based combination treatment dramatically increases therapeutic efficacy in murine globoid cell leukodystrophy.

基于机制的联合治疗显著提高了小鼠球状细胞脑白质营养不良的治疗效果

Hawkins-Salsbury Jacqueline A, Shea Lauren, Jiang Xuntian, Hunter Daniel A, Guzman A Miguel, Reddy Adarsh S, Qin Elizabeth Y, Li Yedda, Gray Steven J, Ory Daniel S, Sands Mark S

Bone marrow transplantation increases efficacy of central nervous system-directed enzyme replacement therapy in the murine model of globoid cell leukodystrophy

在小鼠球状细胞脑白质营养不良模型中,骨髓移植可提高中枢神经系统靶向酶替代疗法的疗效。

Qin, Elizabeth Y; Hawkins-Salsbury, Jacqueline A; Jiang, Xuntian; Reddy, Adarsh S; Farber, Nuri B; Ory, Daniel S; Sands, Mark S