Development of a DUX4-targeting antibody oligonucleotide conjugate as a therapy for FSHD
开发靶向DUX4的抗体寡核苷酸偶联物作为FSHD的治疗方法
期刊:Nucleic Acids Research
影响因子:13.1
doi:10.1093/nar/gkag301
Malecova, Barbora; Sala, David; Melikian, Garineh M; Johns, Rachel; Erdogan, Gulin; Hartmann, Marc; Jordan, Maryam; Arias, Joel Danny; Bhattacharya, Arvind; Meng, Qingying; Dansereau, Oliver; Beppler, Samuel W; Doppalapudi, Venkata R; Huang, Hanhua; Flanagan, William Michael; Levin, Arthur A