日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Impact of patisiran on polyneuropathy of hereditary transthyretin amyloidosis in patients with a V122I or T60A variant: a phase IV multicenter study

帕替西兰对携带 V122I 或 T60A 变异的遗传性转甲状腺素蛋白淀粉样变性患者多发性神经病的影响:一项 IV 期多中心研究

Hussain, Yessar; Malhotra, Saurabh; Sperry, Brett W; Shu, Francy; Ananthasubramaniam, Karthikeyan; Desai, Urvi; Egolum, Ugochukwu; Fernandez, Joel; Freimer, Miriam; Mauricio, Elizabeth; Quan, Dianna; Small, Roy; Capocelli, Kelley; Roblin, Steven; Bender, Shaun; Jay, Patrick Y; Yureneva, Elena; Zolty, Ronald

Safety and Efficacy of Nipocalimab in Patients With Generalized Myasthenia Gravis: Results From the Randomized Phase 2 Vivacity-MG Study

尼波卡利单抗治疗全身型重症肌无力患者的安全性和有效性:来自随机 II 期 Vivacity-MG 研究的结果

Antozzi, Carlo; Guptill, Jeffrey; Bril, Vera; Gamez, Josep; Meuth, Sven G; Nowak, Richard J; Quan, Dianna; Sevilla, Teresa; Jouvin, Marie-Helene; Jin, Jim; Karcher, Keith; Ramchandren, Sindhu; Sun, Hong; Ling, Leona; Zhu, Yaowei; Arroyo, Santiago

Impact of Baseline Neuropathy Severity on Vutrisiran Treatment Response in the Phase 3 HELIOS-A Study

基线神经病变严重程度对 Vutrisiran 治疗反应的影响(HELIOS-A 3 期研究)

Luigetti, Marco; Quan, Dianna; Berk, John L; Conceição, Isabel; Misumi, Yohei; Chao, Chi-Chao; Bender, Shaun; Aldinc, Emre; Vest, John; Adams, David

Practical Guidance for the Use of Patisiran in the Management of Polyneuropathy in Hereditary Transthyretin-Mediated Amyloidosis

帕替西兰在遗传性转甲状腺素蛋白介导的淀粉样变性多发性神经病治疗中的应用实用指南

Dixon, Stacy; Kang, Xuan; Quan, Dianna

Phase 2 Trial of Rituximab in Acetylcholine Receptor Antibody-Positive Generalized Myasthenia Gravis: The BeatMG Study

利妥昔单抗治疗乙酰胆碱受体抗体阳性全身型重症肌无力的 II 期临床试验:BeatMG 研究

Nowak, Richard J; Coffey, Christopher S; Goldstein, Jonathan M; Dimachkie, Mazen M; Benatar, Michael; Kissel, John T; Wolfe, Gil I; Burns, Ted M; Freimer, Miriam L; Nations, Sharon; Granit, Volkan; Smith, A Gordon; Richman, David P; Ciafaloni, Emma; Al-Lozi, Muhammad T; Sams, Laura Ann; Quan, Dianna; Ubogu, Eroboghene; Pearson, Brenda; Sharma, Aditi; Yankey, Jon W; Uribe, Liz; Shy, Michael; Amato, Anthony A; Conwit, Robin; O'Connor, Kevin C; Hafler, David A; Cudkowicz, Merit E; Barohn, Richard J

Patient Assisted Intervention for Neuropathy: Comparison of Treatment in Real Life Situations (PAIN-CONTRoLS): Bayesian Adaptive Comparative Effectiveness Randomized Trial

患者辅助干预治疗神经病变:真实情境下治疗的比较(疼痛控制):贝叶斯自适应比较效果随机试验

Barohn, Richard J; Gajewski, Byron; Pasnoor, Mamatha; Brown, Alexandra; Herbelin, Laura L; Kimminau, Kim S; Mudaranthakam, Dinesh Pal; Jawdat, Omar; Dimachkie, Mazen M; Iyadurai, Stanley; Stino, Amro; Kissel, John; Pascuzzi, Robert; Brannagan, Thomas; Wicklund, Matthew; Ahmed, Aiesha; Walk, David; Smith, Gordon; Quan, Dianna; Heitzman, Darryl; Tobon, Alejandro; Ladha, Shafeeq; Wolfe, Gil; Pulley, Michael; Hayat, Ghazala; Li, Yuebing; Thaisetthawatkul, Pariwat; Lewis, Richard; Biliciler, Suur; Sharma, Khema; Salajegheh, Kian; Trivedi, Jaya; Mallonee, William; Burns, Ted; Jacoby, Mark; Bril, Vera; Vu, Tuan; Ramchandren, Sindhu; Bazant, Mark; Austin, Sara; Karam, Chafic; Hussain, Yessar; Kutz, Christen; Twydell, Paul; Scelsa, Stephen; Kushlaf, Hani; Wymer, James; Hehir, Michael; Kolb, Noah; Ralph, Jeffrey; Barboi, Alexandru; Verma, Navin; Ahmed, Moiz; Memon, Anza; Saperstein, David; Lou, Jau-Shin; Swenson, Andrea; Cash, Tiyonnoh

A Phase 2, Double-Blind, Randomized, Dose-Ranging Trial Of Reldesemtiv In Patients With ALS

一项针对肌萎缩侧索硬化症(ALS)患者的瑞德西姆替夫(Reldesemtiv)II期双盲随机剂量范围试验。

Shefner, Jeremy M; Andrews, Jinsy A; Genge, Angela; Jackson, Carlayne; Lechtzin, Noah; Miller, Timothy M; Cockroft, Bettina M; Meng, Lisa; Wei, Jenny; Wolff, Andrew A; Malik, Fady I; Bodkin, Cynthia; Brooks, Benjamin R; Caress, James; Dionne, Annie; Fee, Dominic; Goutman, Stephen A; Goyal, Namita A; Hardiman, Orla; Hayat, Ghazala; Heiman-Patterson, Terry; Heitzman, Daragh; Henderson, Robert D; Johnston, Wendy; Karam, Chafic; Kiernan, Matthew C; Kolb, Stephen J; Korngut, Lawrence; Ladha, Shafeeq; Matte, Genevieve; Mora, Jesus S; Needham, Merrilee; Oskarsson, Bjorn; Pattee, Gary L; Pioro, Erik P; Pulley, Michael; Quan, Dianna; Rezania, Kourosh; Schellenberg, Kerri L; Schultz, David; Shoesmith, Christen; Simmons, Zachary; Statland, Jeffrey; Sultan, Shumaila; Swenson, Andrea; Berg, Leonard H Van Den; Vu, Tuan; Vucic, Steve; Weiss, Michael; Whyte-Rayson, Ashley; Wymer, James; Zinman, Lorne; Rudnicki, Stacy A

Intensive care unit-acquired weakness: implications for physical therapist management

重症监护室获得性肌无力:对物理治疗师管理的影响

Nordon-Craft, Amy; Moss, Marc; Quan, Dianna; Schenkman, Margaret

Impact of rituximab-associated B-cell defects on West Nile virus meningoencephalitis in solid organ transplant recipients

利妥昔单抗相关B细胞缺陷对实体器官移植受者西尼罗病毒脑膜脑炎的影响

Levi, Marilyn E; Quan, Dianna; Ho, Joseph T; Kleinschmidt-Demasters, B K; Tyler, Kenneth L; Grazia, Todd J

Duplication within the SEPT9 gene associated with a founder effect in North American families with hereditary neuralgic amyotrophy.

SEPT9 基因的重复与北美遗传性神经痛性肌萎缩症家族的创始人效应有关

Landsverk Megan L, Ruzzo Elizabeth K, Mefford Heather C, Buysse Karen, Buchan Jillian G, Eichler Evan E, Petty Elizabeth M, Peterson Esther A, Knutzen Dana M, Barnett Karen, Farlow Martin R, Caress Judy, Parry Gareth J, Quan Dianna, Gardner Kathy L, Hong Ming, Simmons Zachary, Bird Thomas D, Chance Phillip F, Hannibal Mark C