Identification of a myotropic AAV by massively parallel in vivo evaluation of barcoded capsid variants
通过大规模并行体内评估条形码衣壳变体来鉴定肌向性 AAV
期刊:Nature Communications
影响因子:14.7
doi:10.1038/s41467-020-19230-w
Jonas Weinmann, Sabrina Weis, Josefine Sippel, Warut Tulalamba, Anca Remes, Jihad El Andari, Anne-Kathrin Herrmann, Quang H Pham, Christopher Borowski, Susanne Hille, Tanja Schönberger, Norbert Frey, Martin Lenter, Thierry VandenDriessche, Oliver J Müller, Marinee K Chuah, Thorsten Lamla, Dirk Grimm