日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Sleeping Beauty mRNA-LNP enables stable rAAV transgene expression in mouse and NHP hepatocytes and improves vector potency.

Sleeping Beauty mRNA-LNP 可在小鼠和 NHP 肝细胞中实现稳定的 rAAV 转基因表达,并提高载体效力

Zakas Philip M, Cunningham Sharon C, Doherty Ann, van Dijk Eva B, Ibraheim Raed, Yu Stephanie, Mekonnen Befikadu D, Lang Brendan, English Elizabeth J, Sun Gang, Duncan Miles C, Benczkowski Matthew S, Altshuler Robert C, Singh Malvenderjit Jagjit, Kibbler Emily S, Tonga Gulen Y, Wang Zi Jun, Wang Z Jane, Li Guangde, An Ding, Rottman James B, Bhavsar Yashvi, Purcell Cormac, Jain Rachit, Alberry Ryan, Roquet Nathaniel, Fu Yanfang, Citorik Robert J, Rubens Jacob R, Holmes Michael C, Cotta-Ramusino Cecilia, Querbes William, Alexander Ian E, Salomon William E

Correction for Querbes et al., "A JC Virus-Induced Signal Is Required for Infection of Glial Cells by a Clathrin- and eps15-Dependent Pathway"

对 Querbes 等人的文章“JC 病毒诱导的信号是网格蛋白和 eps15 依赖性途径感染神经胶质细胞所必需的”的更正

Querbes, W; Benmerah, A; Tosoni, D; Di Fiore, P P; Atwood, Walter J

Role of angiopoietin-like 3 (ANGPTL3) in regulating plasma level of low-density lipoprotein cholesterol.

血管生成素样蛋白 3 (ANGPTL3) 在调节血浆低密度脂蛋白胆固醇水平中的作用

Xu Yu-Xin, Redon Valeska, Yu Haojie, Querbes William, Pirruccello James, Liebow Abigail, Deik Amy, Trindade Kevin, Wang Xiao, Musunuru Kiran, Clish Clary B, Cowan Chad, Fizgerald Kevin, Rader Daniel, Kathiresan Sekar

Banned from the sharing economy: an agent-based model of a peer-to-peer marketplace for consumer goods and services

被禁止参与共享经济:基于代理的点对点消费品和服务市场模型

Querbes, Adrien

Patient Perspective on Acute Intermittent Porphyria with Frequent Attacks: A Disease with Intermittent and Chronic Manifestations

患者视角下的频繁发作型急性间歇性卟啉症:一种具有间歇性和慢性表现的疾病

Simon, Amy; Pompilus, Farrah; Querbes, William; Wei, Alex; Strzok, Sara; Penz, Craig; Howe, Desiree Lyon; Hungate, Jessica R; Kim, Jae B; Agarwal, Sonalee; Marquis, Patrick

An Investigational RNAi Therapeutic Targeting Glycolate Oxidase Reduces Oxalate Production in Models of Primary Hyperoxaluria

针对乙醇酸氧化酶的在研 RNAi 疗法可减少原发性高草酸尿症模型中的草酸生成

Abigail Liebow, Xingsheng Li, Timothy Racie, Julia Hettinger, Brian R Bettencourt, Nader Najafian, Patrick Haslett, Kevin Fitzgerald, Ross P Holmes, David Erbe, William Querbes, John Knight

Evolving user needs and late-mover advantage

不断变化的用户需求和后发优势

Querbes, Adrien; Frenken, Koen

Metabolism of (13)C5-hydroxyproline in mouse models of Primary Hyperoxaluria and its inhibition by RNAi therapeutics targeting liver glycolate oxidase and hydroxyproline dehydrogenase

原发性高草酸尿症小鼠模型中 (13)C5-羟脯氨酸的代谢及其通过针对肝乙醇酸氧化酶和羟脯氨酸脱氢酶的 RNAi 疗法抑制

Xingsheng Li, John Knight, Sonia Fargue, Brianna Buchalski, Zhengrong Guan, Edward W Inscho, Abigail Liebow, Kevin Fitzgerald, William Querbes, W Todd Lowther, Ross P Holmes

Preclinical Development of a Subcutaneous ALAS1 RNAi Therapeutic for Treatment of Hepatic Porphyrias Using Circulating RNA Quantification

使用循环 RNA 定量技术进行皮下 ALAS1 RNAi 治疗肝卟啉症的临床前开发

Amy Chan, Abigail Liebow, Makiko Yasuda, Lin Gan, Tim Racie, Martin Maier, Satya Kuchimanchi, Don Foster, Stuart Milstein, Klaus Charisse, Alfica Sehgal, Muthiah Manoharan, Rachel Meyers, Kevin Fitzgerald, Amy Simon, Robert J Desnick, William Querbes

Lipopeptide nanoparticles for potent and selective siRNA delivery in rodents and nonhuman primates

用于在啮齿动物和非人灵长类动物中高效选择性递送siRNA的脂肽纳米颗粒

Dong, Yizhou; Love, Kevin T; Dorkin, J Robert; Sirirungruang, Sasilada; Zhang, Yunlong; Chen, Delai; Bogorad, Roman L; Yin, Hao; Chen, Yi; Vegas, Arturo J; Alabi, Christopher A; Sahay, Gaurav; Olejnik, Karsten T; Wang, Weiheng; Schroeder, Avi; Lytton-Jean, Abigail K R; Siegwart, Daniel J; Akinc, Akin; Barnes, Carmen; Barros, Scott A; Carioto, Mary; Fitzgerald, Kevin; Hettinger, Julia; Kumar, Varun; Novobrantseva, Tatiana I; Qin, June; Querbes, William; Koteliansky, Victor; Langer, Robert; Anderson, Daniel G