日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Correction: Harnessing ExDNA for precision Exatecan delivery in cancer: a novel antibody-drug conjugate approach

更正:利用ExDNA实现癌症中Exatecan的精准递送:一种新型抗体-药物偶联物方法

Ianniello, Zaira; Lu, Huimei; Quijano, Elias; Colón-Ríos, Daniel A; Rackear, Madison; Bommireddy, Venu; Ludwig, Dale L; Shen, Zhiyuan; Glazer, Peter M

Harnessing ExDNA for precision exatecan delivery in cancer: a novel antibody-drug conjugate approach.

利用 ExDNA 实现癌症中精准的依沙替康递送:一种新型抗体药物偶联物方法。

Ianniello Zaira, Lu Huimei, Quijano Elias, Colón-Ríos Daniel A, Rackear Madison, Bommireddy Venu, Ludwig Dale L, Shen Zhiyuan, Glazer Peter M

Systemic administration of an RNA binding and cell-penetrating antibody targets therapeutic RNA to multiple mouse models of cancer.

系统性地施用一种 RNA 结合和细胞穿透抗体,将治疗性 RNA 靶向应用于多种小鼠癌症模型

Quijano Elias, Martinez-Saucedo Diana, Ianniello Zaira, Pinto-Medici Natasha, Rackear Madison, Chen Haoting, Lola-Pereira Luiz, Liu Yanfeng, Hegan Denise, Shan Xinning, Tseng Robert, Yugawa Deanne, Chowdhury Sumedha, Khang Minsoo, Singh Jay P, Abdullah Rashed, Azhir Perisa, Kashima Soki, Woods Wendy S, Gosstola Nicholas, Turner Bruce C, Squinto Stephen, Ludwig Dale L, Bindra Ranjit S, Robert Marie E, Braun David A, Perez Pinera Pablo, Saltzman W Mark, Escobar-Hoyos Luisa F, Glazer Peter M

Systemic in utero gene editing as a treatment for cystic fibrosis

系统性子宫内基因编辑作为囊性纤维化的治疗方法

Ricciardi, Adele S; Barone, Christina; Putman, Rachael; Quijano, Elias; Gupta, Anisha; Nguyen, Richard; Mandl, Hanna; Piotrowski-Daspit, Alexandra S; Lopez-Giraldez, Francesc; Luks, Valerie; Freedman-Weiss, Mollie R; Farrelly, James; Ahle, Samantha; Lynn, Anna Y; Glazer, Peter M; Saltzman, W Mark; Stitelman, David H; Egan, Marie E

Next generation triplex-forming PNAs for site-specific genome editing of the F508del CFTR mutation

用于F508del CFTR突变位点特异性基因组编辑的新一代三链体形成PNA

Gupta, Anisha; Barone, Christina; Quijano, Elias; Piotrowski-Daspit, Alexandra S; Perera, J Dinithi; Riccardi, Adele; Jamali, Haya; Turchick, Audrey; Zao, Weixi; Saltzman, W Mark; Glazer, Peter M; Egan, Marie E

DNA recognition and induced genome modification by a hydroxymethyl-γ tail-clamp peptide nucleic acid

羟甲基-γ尾钳肽核酸对DNA的识别和诱导基因组修饰

Oyaghire, Stanley N; Quijano, Elias; Perera, J Dinithi R; Mandl, Hanna K; Saltzman, W Mark; Bahal, Raman; Glazer, Peter M

Antisense Oligonucleotides: An Emerging Area in Drug Discovery and Development

反义寡核苷酸:药物发现与开发领域的新兴方向

Dhuri, Karishma; Bechtold, Clara; Quijano, Elias; Pham, Ha; Gupta, Anisha; Vikram, Ajit; Bahal, Raman

In utero nanoparticle delivery for site-specific genome editing

利用纳米颗粒在子宫内进行位点特异性基因组编辑

Ricciardi, Adele S; Bahal, Raman; Farrelly, James S; Quijano, Elias; Bianchi, Anthony H; Luks, Valerie L; Putman, Rachael; López-Giráldez, Francesc; Coşkun, Süleyman; Song, Eric; Liu, Yanfeng; Hsieh, Wei-Che; Ly, Danith H; Stitelman, David H; Glazer, Peter M; Saltzman, W Mark

Nanoparticles that deliver triplex-forming peptide nucleic acid molecules correct F508del CFTR in airway epithelium

递送三链体形成肽核酸分子的纳米颗粒可纠正气道上皮细胞中的F508del CFTR突变。

McNeer, Nicole Ali; Anandalingam, Kavitha; Fields, Rachel J; Caputo, Christina; Kopic, Sascha; Gupta, Anisha; Quijano, Elias; Polikoff, Lee; Kong, Yong; Bahal, Raman; Geibel, John P; Glazer, Peter M; Saltzman, W Mark; Egan, Marie E

Single-stranded γPNAs for in vivo site-specific genome editing via Watson-Crick recognition

利用Watson-Crick识别技术进行体内位点特异性基因组编辑的单链γPNA

Bahal, Raman; Quijano, Elias; McNeer, Nicole A; Liu, Yanfeng; Bhunia, Dinesh C; Lopez-Giraldez, Francesco; Fields, Rachel J; Saltzman, William M; Ly, Danith H; Glazer, Peter M