Home infusion program with enzyme replacement therapy for Fabry disease: The experience of a large Italian collaborative group
法布里病酶替代疗法居家输液项目:意大利大型合作组的经验
期刊:Molecular Genetics and Metabolism Reports
影响因子:1.9
doi:10.1016/j.ymgmr.2017.06.005
Concolino, D; Amico, L; Cappellini, M D; Cassinerio, E; Conti, M; Donati, M A; Falvo, F; Fiumara, A; Maccarone, M; Manna, R; Matucci, A; Musumeci, M B; Nicoletti, A; Nisticò, R; Papadia, F; Parini, R; Peluso, D; Pensabene, L; Pisani, A; Pistone, G; Rigoldi, M; Romani, I; Tenuta, M; Torti, G; Veroux, M; Zachara, E