日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Menin inhibition with revumenib for NPM1-mutated relapsed or refractory acute myeloid leukemia: the AUGMENT-101 study

使用revumenib抑制Menin治疗NPM1突变复发或难治性急性髓系白血病:AUGMENT-101研究

Arellano, Martha L; Thirman, Michael J; DiPersio, John F; Heiblig, Maël; Stein, Eytan M; Schuh, Andre C; Žučenka, Andrius; de Botton, Stephane; Grove, Carolyn S; Mannis, Gabriel N; Papayannidis, Cristina; Perl, Alexander E; Issa, Ghayas C; Aldoss, Ibrahim; Bajel, Ashish; Dickens, David S; Kühn, Michael W M; Mantzaris, Ioannis; Raffoux, Emmanuel; Traer, Elie; Amitai, Irina; Döhner, Hartmut; Greco, Corinna; Kovacsovics, Tibor; McMahon, Christine M; Montesinos, Pau; Pigneux, Arnaud; Shami, Paul J; Stone, Richard M; Wolach, Ofir; Harpel, John G; Chudnovsky, Yakov; Yu, Li; Bagley, Rebecca G; Smith, Angela R; Blachly, James S

Long-term follow-up and combined Phase 2 results of eprenetapopt and azacitidine in patients with TP53 mutant MDS/AML

长期随访及eprenetapopt联合阿扎胞苷治疗TP53突变型MDS/AML患者的II期联合试验结果

Sallman, David A; Komrokji, Rami S; Dezern, Amy E; Sebert, Marie; Garcia-Manero, Guillermo; Rahmé, Ramy; Winer, Eric S; Lehmann-Che, Jacqueline; Roboz, Gail J; Madelaine, Isabelle; Sekeres, Mikkael A; Peterlin, Pierre; Chan, Onyee; Beyne-Rauzy, Odile; Kuykendall, Andrew; Recher, Christian; McLemore, Amy; Stamatoullas, Aspasia; Zhang, Ling; Willems, Lise; Mo, Qianxing; Raffoux, Emmanuel; Nardelli, Lisa; Berthon, Céline; Al Ali, Najla H; Quesnel, Bruno; Padron, Eric; Kantarjian, Hagop M; List, Alan F; Ades, Lionel; Lancet, Jeffrey E; Fenaux, Pierre; Cluzeau, Thomas

Inflammatory disorders in IDH-mutated myeloid neoplasms: Characteristics and response to IDH inhibitors

IDH突变型髓系肿瘤的炎症性疾病:特征及对IDH抑制剂的反应

Stammler, Romain; Chen, Peter; Debeaupuis, Orianne; Zhao, Lin-Pierre; Ruyer-Thompson, Mirabelle; Zakine, Eve; Rossignol, Julien; Goldwirt, Lauriane; Comont, Thibault; Heiblig, Maël; Adès, Lionel; Sebert, Marie; Allain, Jean-Sébastien; Campagne, Julien; Couturier, Marie-Anne; Cumin, Marina; Dalmas, Marie-Caroline; Denis, Guillaume; Devloo, Cécile; De Voeght, Adrien; Drevon, Louis; Duffau, Pierre; Georgin-Lavialle, Sophie; Gobert, Delphine; Kosmider, Olivier; Rieux-Laucat, Frédéric; Abisror, Noémie; Lazaro, Estibaliz; Lopez, Jean-Guillaume; Maria, Alexandre; Mauhin, Wladimir; Merindol, Julie; Merlot, Claire; Mirault, Tristan; Pascal, Laurent; Perrin, François; Raffoux, Emmanuel; Rahme, Ramy; Roos-Weil, Damien; Terrier, Benjamin; Thoreau, Benjamin; Fain, Olivier; Fenaux, Pierre; Hirsch, Pierre; Jachiet, Vincent; Hadjadj, Jérôme; Mékinian, Arsène

Exposure toxicity of venetoclax in acute myeloid leukemia patients in the real-life setting: impact of high exposure on delayed neutropenia

真实世界中急性髓系白血病患者使用维奈托克的暴露毒性:高暴露对迟发性中性粒细胞减少症的影响

Puisset, Florent; Raffoux, Emmanuel; Ades, Lionel; Huynh, Tony; Itzykson, Raphaël; Bouscary, Didier; Aguinana, Loréa; Rabian, Florence; Sebert, Marie; Vekhoff, Anne; Brissot, Eolia; Mohty, Mohamad; Bonnin, Agnes; Genthon, Alexis; Zerbit, Jeremie; Willems, Lise; Decrocq, Justine; Contejean, Adrien; Lengline, Etienne; Mourah, Samia; Goldwirt, Lauriane

Prognostic significance of monocytic-like phenotype in patients with AML treated with venetoclax and azacytidine

单核细胞样表型在接受维奈托克和阿扎胞苷治疗的急性髓系白血病患者中的预后意义

Zhao, Lin-Pierre; Dumas-Rivero, Typhaine; Barette, Lauren; Aguinaga, Lorea; Cheffai, Arij; Chauvel, Clémentine; Dal Bello, Reinaldo; Raffoux, Emmanuel; Clappier, Emmanuelle; Duchmann, Matthieu; Fenaux, Pierre; Lemaire, Pierre; Mathis, Stephanie; Sébert, Marie; Adès, Lionel; Itzykson, Raphaël

Long-term real-world evidence of CPX-351 of high-risk patients with AML identified high rate of negative MRD and prolonged OS

CPX-351治疗高危急性髓系白血病(AML)患者的长期真实世界证据表明,该疗法可显著提高微小残留病灶(MRD)阴性率并延长总生存期(OS)。

Cluzeau, Thomas; Guolo, Fabio; Chiche, Edmond; Minetto, Paola; Rahme, Ramy; Bertoli, Sarah; Fianchi, Luana; Micol, Jean-Baptiste; Gottardi, Michele; Peterlin, Pierre; Galimberti, Sara; Thomas, Xavier; Rizzuto, Giuliana; Legrand, Olivier; Rondoni, Michela; Raffoux, Emmanuel; Bertani, Giambattista; Caulier, Alexis; D'Argenio, Michelina; Bonmati, Caroline; Billio, Atto; Lejeune, Caroline; Scappini, Barbara; Pigneux, Arnaud; Zappasodi, Patrizia; Recher, Christan; Grimaldi, Francesco; Ades, Lionel; Lemoli, Roberto M

Asciminib for relapsed or refractory Philadelphia chromosome-positive acute lymphoblastic leukemia

Asciminib 用于治疗复发或难治性费城染色体阳性急性淋巴细胞白血病

Chanut, Mathilde; Cabannes-Hamy, Aurélie; Balsat, Marie; Sahki, Nassim; Raffoux, Emmanuel; Hicheri, Yosr; Lioure, Bruno; Laemmel, Lucie; Leguay, Thibaut; Cacheux, Victoria; Gallego-Hernanz, Maria Pilar; Pieragostini, Andrea; Roth-Guepin, Gabrielle; Gabellier, Ludovic; Denizon, Nathalie; Willems, Lise; Cabrera, Quentin; Chantepie, Sylvain; Coiteux, Valérie; Capdupuy, Claudie; Carré, Martin; Machet, Antoine; Lambert, Juliette; Roux, Sandrine; Nicolini, Franck-Emmanuel; Boissel, Nicolas; Clappier, Emmanuelle; Kim, Rathana; Rousselot, Philippe

AML patient blasts exhibit polarization defects upon interaction with bone marrow stromal cells.

急性髓系白血病患者的原始细胞在与骨髓基质细胞相互作用时表现出极化缺陷

Saadallah Khansa, Vianay Benoît, Bonnemay Louise, Pasquer Hélène, Kelly Lois, Mathis Stéphanie, Culeux Cécile, Marie Raphael, Meslin Paul Arthur, Fodil Sofiane, Chaintreuil Paul, Kerreneur Emeline, Jacquel Arnaud, Raffoux Emmanuel, Nizard Rémy, Lobry Camille, Blanchoin Laurent, Benajiba Lina, Théry Manuel

A phase 1, first-in-human, dose-escalation study of JNJ-74856665 (dihydroorotate dehydrogenase inhibitor) alone or in combination in patients with AML or MDS

一项针对急性髓系白血病 (AML) 或骨髓增生异常综合征 (MDS) 患者的 I 期、首次人体剂量递增研究,旨在评估 JNJ-74856665(二氢乳清酸脱氢酶抑制剂)单药或联合用药的疗效。

Searle, Emma; Cluzeau, Thomas; O'Nions, Jenny; Recher, Christian; Gyan, Emmanuel; Morillo, Daniel; Esteve, Jordi; Kulasekararaj, Austin; Raffoux, Emmanuel; Walter, Harriet S; Pigneux, Arnaud; Valcárcel, David; Daskalakis, Nikki; Bussolari, Jacqueline; Pietsch, E Christine; Kuduk, Scott; Bush, Tammy; Zhang, Xiaochun; Philippar, Ulrike; Oluwasanjo, Adetokunbo; Bradford, Kathryn; Miller, Jonathan; Van Bogaert, Charlotte; Curtis, Martin; Chang, Shih-Yu; Guttke, Christina; Gaj, Stan; Pearson, Rachel; Murphy, Joseph; van Dijck, Wim; Alfonso Piérola, Ana

Contribution of paranasal sinus, chest, and abdomen/pelvis computed tomography in patients with febrile neutropenia

鼻窦、胸部和腹部/盆腔计算机断层扫描在发热性中性粒细胞减少症患者中的作用

Tran, Charles; de Kerviler, Éric; Bergeron, Anne; Raffoux, Emmanuel; Xhaard, Aliénor; de Bazelaire, Cédric; de Margerie-Mellon, Constance