Targeted gene editing and near-universal cDNA insertion of CYBA and CYBB as a treatment for chronic granulomatous disease
靶向基因编辑和近乎普遍的 CYBA 和 CYBB cDNA 插入作为慢性肉芽肿病的治疗方法
期刊:Nature Communications
影响因子:15.7
doi:10.1038/s41467-025-62738-2
Wolff, Jonas Holst; Skov, Thomas Wisbech; Haslund, Didde; Dorset, Sofie Rahbek; Revenfeld, Anne Louise S; Aussel, Clotilde; Jørgensen, Sofie E; Holm, Mette; Thomsen, Martin K; Ammann, Sandra; Cathomen, Toni; Mogensen, Trine H; Møller, Bjarne Kuno; Bak, Rasmus O; Mikkelsen, Jacob Giehm