Novel Orthogonally Hydrocarbon-Modified Cell-Penetrating Peptide Nanoparticles Mediate Efficient Delivery of Splice-Switching Antisense Oligonucleotides In Vitro and In Vivo
新型正交烃修饰的细胞穿透肽纳米粒子介导剪接转换反义寡核苷酸在体内和体外的有效递送
期刊:Biomedicines
影响因子:3.9
doi:10.3390/biomedicines9081046
Safa Bazaz, Tõnis Lehto, Rahel Tops, Olof Gissberg, Dhanu Gupta, Burcu Bestas, Jeremy Bost, Oscar P B Wiklander, Helena Sork, Eman M Zaghloul, Doste R Mamand, Mattias Hällbrink, Rannar Sillard, Osama Saher, Kariem Ezzat, C I Edvard Smith, Samir El Andaloussi, Taavi Lehto