Multicenter phase 2 trial of sirolimus for tuberous sclerosis: kidney angiomyolipomas and other tumors regress and VEGF- D levels decrease
雷帕霉素治疗结节性硬化症的多中心 2 期试验:肾血管平滑肌脂肪瘤和其他肿瘤消退,VEGF- D 水平下降
期刊:PLoS One
影响因子:2.9
doi:10.1371/journal.pone.0023379
Sandra L Dabora, David Neal Franz, Stephen Ashwal, Arthur Sagalowsky, Francis J DiMario Jr, Daniel Miles, Drew Cutler, Darcy Krueger, Raul N Uppot, Rahmin Rabenou, Susana Camposano, Jan Paolini, Fiona Fennessy, Nancy Lee, Chelsey Woodrum, Judith Manola, Judy Garber, Elizabeth A Thiele